New approaches to treat PKU: How far are we?

Molecular Genetics and Metabolism

Volumn 81, Issue 1, 2004, Pages 1-2

  Blau, Nenad ^a   Scriver, Charles R ^b  

^a UNIVERSITY OF ZURICH   (Switzerland)

^b RESEARCH INSTITUTE OF THE MCGILL UNIVERSITY HEALTH CENTRE   (Canada)

Author keywords

[No Author keywords available]

Indexed keywords

PHENYLALANINE; PHENYLALANINE 4 MONOOXYGENASE; PHENYLALANINE AMMONIA LYASE; TETRAHYDROBIOPTERIN;

BINDING AFFINITY; BRAIN INJURY; CONCENTRATION (PARAMETERS); DIET RESTRICTION; DIET THERAPY; DRUG COST; GENE DELIVERY SYSTEM; GENE TARGETING; GENE TRANSFER; GENE VECTOR; GENETIC ENGINEERING; HUMAN; HYPERPHENYLALANINEMIA; LACTOCOCCUS LACTIS; METABOLIC DISORDER; MUTATION; NONHUMAN; NOTE; NUTRITION; PATIENT COMPLIANCE; PHENYLKETONURIA; PRIORITY JOURNAL; PROTEIN DEGRADATION; PROTEIN EXPRESSION; SOMATIC GENE THERAPY; VIRAL GENE THERAPY;

LACTOCOCCUS LACTIS; STREPTOCOCCUS;

EID: 0346059414     PISSN: 10967192     EISSN: None     Source Type: Journal    
DOI: 10.1016/j.ymgme.2003.09.011     Document Type: Note

References (9)

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