Human gene therapy - A new era in medicine

Emirates Medical Journal

Volumn 20, Issue 2, 2002, Pages 107-109

  Friedmann, Theodore ^a  

^a UNIVERSITY OF CALIFORNIA   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

RECOMBINANT DNA;

ACQUIRED IMMUNE DEFICIENCY SYNDROME; AGING; ARTHRITIS; BACTERIOPHAGE; CANCER; CARDIOVASCULAR DISEASE; CYSTIC FIBROSIS; CYSTINOSIS; DEGENERATIVE DISEASE; DIABETES MELLITUS; ENVIRONMENTAL FACTOR; GENE EXPRESSION; GENE IDENTIFICATION; GENE MUTATION; GENE THERAPY; GENE TRANSFER; HEART DISEASE; HEREDITY; HUMAN GENOME; HUNTINGTON CHOREA; INFECTION; LESCH NYHAN SYNDROME; METABOLIC DISORDER; MOLECULAR CLONING; NEUROLOGIC DISEASE; NUCLEOTIDE SEQUENCE; RETINOBLASTOMA; REVIEW; SICKLE CELL ANEMIA; TAY SACHS DISEASE;

EID: 0345974514     PISSN: 02506882     EISSN: None     Source Type: Journal    
DOI: None     Document Type: Review

References (7)

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2. McPherson JD, Marra M, Hillier L, et al: A physical map of the human genome. Nature, 2001; 409: 934-941.
3. Friedmann T and Roblin R: Gene therapy for human genetic disease? Science, 1972; 175: 949-955.
4. Cavazzana-Calvo M, Hacein-Bey S, de Saint Basile G, et al: Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease. Science. 2000; 288: 669-672.
5. Kay MA, Manno CS, Ragni MV, et al: Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AA V vector. Nature Genetics, 2000; 24:257-261.
6. Kay MA and High K: Gene therapy for the hemophilias. Proc Natl Acad Sc USA, 96; 2000; 9973-9975.
7. Friedmann T: Principles for human gene therapy studies. Science, 2000; 287: 2163-2165.