-
1
-
-
0034161486
-
Sustained expression of human factor VIII in mice using a parvovirus-based vector
-
Chao H, Mao L, Bruce A,Walsh C. Sustained expression of human factor VIII in mice using a parvovirus-based vector. Blood 2000; 95: 1594-9.
-
(2000)
Blood
, vol.95
, pp. 1594-1599
-
-
Chao, H.1
Mao, L.2
Bruce, A.3
Walsh, C.4
-
2
-
-
0033978147
-
AAV vectors: is clinical success on the horizon?
-
Monahan P, Samulski R. AAV vectors: is clinical success on the horizon? Gene Ther 2000; 7: 24-30.
-
(2000)
Gene Ther
, vol.7
, pp. 24-30
-
-
Monahan, P.1
Samulski, R.2
-
3
-
-
0032853699
-
Immune responses to adenovirus and adeno-associated virus in humans
-
Chirmule N, Propert K, Magosin S, Qian Y, Qian R, Wilson J. Immune responses to adenovirus and adeno-associated virus in humans. Gene Ther 1999; 6: 1574-83.
-
(1999)
Gene Ther
, vol.6
, pp. 1574-1583
-
-
Chirmule, N.1
Propert, K.2
Magosin, S.3
Qian, Y.4
Qian, R.5
Wilson, J.6
-
4
-
-
0034830365
-
Observed incidence of tumorigenesis in long-term rodent studies of rAAV vectors
-
Donsante A, Vogler C, Muzyczka N, Crawford J, Barker J, Flotte T, Campbell-Thompson M, Daly T, Sands M. Observed incidence of tumorigenesis in long-term rodent studies of rAAV vectors. Gene Ther 2001; 8: 1343-6.
-
(2001)
Gene Ther
, vol.8
, pp. 1343-1346
-
-
Donsante, A.1
Vogler, C.2
Muzyczka, N.3
Crawford, J.4
Barker, J.5
Flotte, T.6
Campbell-Thompson, M.7
Daly, T.8
Sands, M.9
-
5
-
-
0034050904
-
Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector
-
Kay M, Manno C, Ragni M, Larson P, Couto L, McClelland A, Glader B, Chew A, Tai S, Herzog R, Arruda V, Johnson F, Scallan C, Skarsgard E, Flake A, High K. Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector. Nat Genet 2000; 24: 257-61.
-
(2000)
Nat Genet
, vol.24
, pp. 257-261
-
-
Kay, M.1
Manno, C.2
Ragni, M.3
Larson, P.4
Couto, L.5
McClelland, A.6
Glader, B.7
Chew, A.8
Tai, S.9
Herzog, R.10
Arruda, V.11
Johnson, F.12
Scallan, C.13
Skarsgard, E.14
Flake, A.15
High, K.16
-
6
-
-
0034842912
-
Sustained and complete phenotype correction of hemophilia b mice following intramuscular injection of aav1serotype vectors
-
Chao H, Monahan P, Liu Y, Samulski R, Walsh C. Sustained and complete phenotype correction of hemophilia b mice following intramuscular injection of aav1serotype vectors. Mol Ther 2001; 4: 217-22.
-
(2001)
Mol Ther
, vol.4
, pp. 217-222
-
-
Chao, H.1
Monahan, P.2
Liu, Y.3
Samulski, R.4
Walsh, C.5
-
7
-
-
0031897270
-
Human gene targeting by viral vectors
-
Russell D, Hirata R. Human gene targeting by viral vectors. Nat Genet 1998; 18: 325-30.
-
(1998)
Nat Genet
, vol.18
, pp. 325-330
-
-
Russell, D.1
Hirata, R.2
-
8
-
-
0037134020
-
A system for stable expression of short interefering RNAs in mammalian cells
-
Brummelkamp T, Bernards R, Agami R. A system for stable expression of short interefering RNAs in mammalian cells. Science 2002; 296: 550-3.
-
(2002)
Science
, vol.296
, pp. 550-553
-
-
Brummelkamp, T.1
Bernards, R.2
Agami, R.3
-
9
-
-
0032993842
-
Spliceosome-mediated RNA trans-splicing as a tool for gene therapy
-
Puttaraju M, Jamison S, Mansfield S, Garcia-Blanco M, Mitchell L. Spliceosome-mediated RNA trans-splicing as a tool for gene therapy. Nat Biotechnol 1999; 17: 246-52.
-
(1999)
Nat Biotechnol
, vol.17
, pp. 246-252
-
-
Puttaraju, M.1
Jamison, S.2
Mansfield, S.3
Garcia-Blanco, M.4
Mitchell, L.5
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