Gene therapy of X-linked severe combined immunodeficiency

Current Opinion in Allergy and Clinical Immunology

Volumn 2, Issue 6, 2002, Pages 507-509

  Cavazzana Calvo, Marina ^a   Hacein Bey Abina, Salima ^a   Fischer, Alain ^a  

^a HÔPITAL NECKER ENFANTS MALADES   (France)

Author keywords

Gene therapy; Hematopoietic stem cell transplantation; Primary immunodeficiencies

Indexed keywords

GENE PRODUCT; IMMUNOGLOBULIN;

ALLOGENIC BONE MARROW TRANSPLANTATION; ALLOTRANSPLANTATION; CLINICAL TRIAL; COMBINED IMMUNODEFICIENCY; GENE SILENCING; GENE THERAPY; GENETIC TRANSDUCTION; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMAN; INTERMETHOD COMPARISON; PRIORITY JOURNAL; REVIEW; T LYMPHOCYTE; THYMUS FUNCTION; X CHROMOSOME LINKED DISORDER;

BONE MARROW TRANSPLANTATION; FEMALE; GENE THERAPY; GENETIC DISEASES, X-LINKED; HUMANS; MALE; PROGNOSIS; RISK ASSESSMENT; SEVERE COMBINED IMMUNODEFICIENCY; STEM CELL TRANSPLANTATION; TRANSPLANTATION, HOMOLOGOUS; TREATMENT OUTCOME;

EID: 0036959269     PISSN: 15284050     EISSN: None     Source Type: Journal    
DOI: 10.1097/00130832-200212000-00005     Document Type: Review

References (11)

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