Pharmacological regulation of protein expression from adeno-associated viral vectors in the eye

Molecular Therapy

Volumn 6, Issue 2, 2002, Pages 238-242

  Auricchio, Alberto ^a   Rivera, Victor M ^c   Clackson, Tim ^c   O'Connor, Erin E ^a   Maguire, Albert M ^b   Tolentino, Michael J ^b   Bennett, Jean ^b   Wilson, James M ^a  

^a WISTAR INSTITUTE   (United States)

^b UNIVERSITY OF PENNSYLVANIA   (United States)

^c ARIAD PHARMACEUTICALS INC   (United States)

Author keywords

AAV; Epo; Nonhuman primate; Rapamycin inducible transcription; Retina

Indexed keywords

BIOCHEMICAL MARKER; ERYTHROPOIETIN; PARVOVIRUS VECTOR; RAPAMYCIN; VIRUS VECTOR;

ADENO ASSOCIATED VIRUS; ANIMAL EXPERIMENT; ANIMAL MODEL; ANTERIOR EYE CHAMBER; ARTICLE; BLOOD EYE BARRIER; CONTROLLED STUDY; DOSE RESPONSE; DRUG EFFECT; DRUG WITHDRAWAL; EYE DISEASE; FEMALE; GENE EXPRESSION REGULATION; GENE INDUCTION; GENE THERAPY; NONHUMAN; PROTEIN ANALYSIS; PROTEIN EXPRESSION; PROTEIN SECRETION; RAT; RETINA DEGENERATION; RETINA DISEASE; RETINA NEOVASCULARIZATION; RHESUS MONKEY; TRANSCRIPTION REGULATION; TRANSGENE; VIRAL GENE DELIVERY SYSTEM;

ADENO-ASSOCIATED VIRUS; ANIMALIA; MACACA MULATTA; PARVOVIRUS; PRIMATES;

EID: 0036664935     PISSN: 15250016     EISSN: None     Source Type: Journal    
DOI: 10.1006/mthe.2002.0660     Document Type: Article

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