Adenovirus-mediated gene therapy in a mouse model of glycogen storage disease type 1a

European Journal of Pediatrics, Supplement

Volumn 161, Issue 1, 2002, Pages

  Chou, Janice Yang ^a   Zingone, Adriana ^a   Pan, Chi Jiunn ^a  

^a EUNICE KENNEDY SHRIVER NATIONAL INSTITUTE OF CHILD HEALTH AND HUMAN DEVELOPMENT   (United States)

Author keywords

Gene therapy; Glucose 6 phosphatase; Glycogen storage disease; GSD 1a mouse model; Recombinant adenovirus

Indexed keywords

ADENOVIRUS VECTOR; CHOLESTEROL; GLUCOSE; GLUCOSE 6 PHOSPHATASE; GLYCOGEN; TRIACYLGLYCEROL; URIC ACID; VIRUS DNA;

BODY GROWTH; CHOLESTEROL BLOOD LEVEL; CONFERENCE PAPER; DRUG INFUSION; ENZYME ACTIVITY; FEASIBILITY STUDY; GENE DELETION; GENE REPLACEMENT THERAPY; GLUCOSE BLOOD LEVEL; GLYCOGEN STORAGE DISEASE TYPE 1; HEPATOMEGALY; KIDNEY HYPERTROPHY; NONHUMAN; PRIORITY JOURNAL; SURVIVAL TIME; TISSUE LEVEL; TRIACYLGLYCEROL BLOOD LEVEL; URIC ACID BLOOD LEVEL; VIRAL GENE THERAPY; VIRUS RECOMBINANT;

EID: 0036392360     PISSN: 09439676     EISSN: None     Source Type: Journal    
DOI: 10.1007/bf02679996     Document Type: Conference Paper

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