Sample size for testing a proportion in clinical trials: A "two-step" procedure combining power and confidence interval expected width

American Statistician

Volumn 55, Issue 4, 2001, Pages 288-292

  Cesana, B M ^a   Reina, G ^b   Marubini, E ^b  

^a FONDAZIONE IRCCS CA GRANDA OSPEDALE MAGGIORE POLICLINICO   (Italy)

^b UNIVERSITY OF MILAN   (Italy)

Author keywords

Binomial distribution; Power and effect estimate; Sample size calculation

Indexed keywords

EID: 0035632947     PISSN: 00031305     EISSN: None     Source Type: Journal    
DOI: 10.1198/000313001753272222     Document Type: Article

References (18)

1. Agresti, A., and Coull, B. A. (1998), "Approximate is Better than 'Exact' for Interval Estimation of Binomial Proportions," The American Statistician, 52, 119-126.
2. Armitage, P., and Berry, G. (1987), Statistical Methods in Medical Research (2nd ed.), Oxford: Blackwell Scientific Publications.
3. Blyth, C. R. (1986), "Approximate Binomial Confidence Limits," Journal of the American Statistical Association, 81, 843-855.
4. Blyth, C. R., and Still, H. A. (1983), "Binomial Confidence Intervals," Journal of the American Statistical Association, 78, 108-116.
5. Borenstein, M. (1994), "Planning for Precision in Survival Studies," Journal of Clinical Epidemiology, 47, 1277-1285.
6. Clopper, C. J., and Pearson, E. S. (1934), "The Use of Confidence or Fiducial Limits Illustrated in the Case of the Binomial," Biometrika, 26, 404-413.
7. Daly, L. (1992), "Simple SAS Macros for the Calculation of Exact Binomial and Poisson Confidence Limits," Computers in Biology and Medicine, 22, 351-361.
8. Feinstein, A. R., and Concato, J. (1998), "The Quest for 'Power': Contradictory Hypotheses and Inflated Sample Sizes," Journal of Clinical Epidemiology, 51, 537-545.
9. Goodman, S. N., and Berlin, J. A. (1994), "The Use of Predicted Confidence Intervals when Planning Experiments and the Misuse of Power when Interpreting Results," Annals of Internal Medicine, 121, 200-206.
10. Hald, A. (1952), Statistical Theory with Engineering Applications, New York: Wiley.
11. Leemis, L. M., and Trivedi, K. S. (1996), "A Comparison of Approximate Interval Estimators for the Bernoulli Parameter," The American Statistician, 50, 63-68.
12. Klotz, J. H. (1996), Comment on "A Comparison of Approximate Interval Estimators for the Bernoulli Parameter" by L. M. Leemis, and K. S. Trivedi, The American Statistician, 50 , 388-389.
13. Mariani, L., and Marubini E. (1996), "Design and Analysis of Phase II Cancer Trials: A Review of Statistical Methods and Guidelines For Medical Researchers," International Statistical Review, 64, 61-88.
14. Newcombe, R. G. (1998), "Two-Sided Confidence Intervals for the Single Proportion: Comparison of Seven Methods," Statistics in Medicine, 17, 857-872.
15. Nicewander, W. A., and Price, J. M. (1997), "A Consonance Criterion for Choosing Sample Size," The American Statistician, 311-317.
16. Rothman, K. (1986), Modern Epidemiology, Boston: Little Brown.
17. Vollset, S. E. (1993), "Confidence Intervals for a Binomial Proportion," Statistics in Medicine, 12, 809-824.
18. _ (1994), Author's reply, Statistics in Medicine, 13, 1284-1285.