Oral megadose methylprednisolone therapy for refractory diamond-blackfan anemia

American Journal of Pediatric Hematology/Oncology

Volumn 23, Issue 6, 2001, Pages 353-356

  Buchanan, George R ^a   Özsolyu, Sinasi ^b   Lipton, Jeffrey ^c   Glader, Bertil ^d   Alter, Blanche ^e   Bernini, Juan Carlos ^f  

^a UNIVERSITY OF TEXAS SOUTHWESTERN MEDICAL CENTER   (United States)

^b Turkish Hlth and Therapy Foundation   (Turkey)

^c MOUNT SINAI SCHOOL OF MEDICINE   (United States)

^d STANFORD UNIVERSITY MEDICAL CENTER   (United States)

^e UNIVERSITY OF TEXAS MEDICAL BRANCH   (United States)

^f Cook Children’s Medical Center ^*  (United States)

Author keywords

Anemia; Diamond Blackfan

Indexed keywords

CORTICOSTEROID; METHYLPREDNISOLONE; PREDNISOLONE;

ADOLESCENT; ARTICLE; BLACKFAN DIAMOND ANEMIA; BLOOD TRANSFUSION; CHILD; CLINICAL ARTICLE; CLINICAL PROTOCOL; CLINICAL TRIAL; DRUG EFFICACY; DRUG MEGADOSE; FEMALE; HEMOGLOBIN DETERMINATION; HUMAN; MALE; MULTICENTER STUDY; PRIORITY JOURNAL; REFRACTORY ANEMIA; RELAPSE; RETICULOCYTE; TOXICITY;

ADMINISTRATION, ORAL; ADOLESCENT; ANEMIA, REFRACTORY; CHILD; CHILD, PRESCHOOL; DOSE-RESPONSE RELATIONSHIP, DRUG; FANCONI ANEMIA; FEMALE; GLUCOCORTICOIDS; HUMANS; MALE; METHYLPREDNISOLONE; PROSPECTIVE STUDIES;

EID: 0034857604     PISSN: 01928562     EISSN: None     Source Type: Journal    
DOI: 10.1097/00043426-200108000-00006     Document Type: Article

References (11)

1. Alter BP, Young NS. The bone marrow failure syndromes. In: Nathan D, Orkin S, eds. Hematology of infancy and childhood, Ed. 5. Philadelphia: WB Saunders, 1998:237-335.
2. Janov AJ, Leong T, Nathan DG, et al. Diamond-Blackfan anemia natural history and sequelae of treatment. Medicine 1996; 75:77-8.
3. Splain J, Berman BW. Cyclosporin A treatment for Diamond-Blackfan anemia. Am J Hematol 1992; 39:208-11.
4. Olivieri NF, Feig SA, Valentino L, et al. Failure of recombinant human interleukin-3 therapy to induce erythropoiesis in patients with refractory Diamond-Blackfan anemia. Blood 1994; 83:2444-50.
5. Greinix HT, Storb R, Sanders JE, et al. Long-term survival and cure after marrow transplantation for congenital hypoplastic anemia (Diamond-Blackfan syndrome). Br J Haematol 1993; 84:515-20.
6. Özsolyu S. High-dose intravenous corticosteroid for a patient with Diamond-Blackfan syndrome refractory to classical prednisone treatment. Acta Haematol 1984; 71:207-10.
7. Özsolyu S. High-dose intravenous corticosteroid treatment for patients with Diamond-Blackfan syndrome resistant or refractory to conventional treatment. Am J Pediatr Hematol Oncol 1988; 10:217-23.
8. Bernini JC, Carrillo JM, Buchanan GR. High-dose intravenous methylprednisolone therapy for patients with Diamond-Blackfan anemia refractory to conventional doses of prednisone. J Pediatr 1995; 127:654-9.
9. Özsolyu S. High-dose intravenous methylprednisolone for constitutional pure red cell aplasia. Blood 1988; 72:1840.
10. Özsolyu S. Megadose methylprednisolone for Diamond-Blackfan anemia. Am J Hematol 1993; 43:335.
11. Özsolyu S. Oral megadose methylprednisolone for treatment of Diamond-Blackfan anaemia. Br J Haematol 1992; 81:135-6.