Prolonged correction of hyperlipidemia in mice with familial hypercholesterolemia using an adeno-associated viral vector expressing very-low-density lipoprotein receptor

Molecular Therapy

Volumn 2, Issue 3, 2000, Pages 256-261

  Chen, Shu Jen ^a   Rader, Daniel J ^a   Tazelaar, John ^a   Kawashiri, Masa Aki ^a   Gao, Guang Ping ^a   Wilson, James M ^a,b  

^a UNIVERSITY OF PENNSYLVANIA   (United States)

^b WISTAR INSTITUTE   (United States)

Author keywords

Cellular immunity; Gene therapy; Liver

Indexed keywords

ADENO-ASSOCIATED VIRUS; ANIMALIA; MURINAE;

LOW DENSITY LIPOPROTEIN RECEPTOR; VERY LOW DENSITY LIPOPROTEIN RECEPTOR;

ADENO ASSOCIATED VIRUS; ANIMAL; ARTICLE; GENE TRANSFER; GENE VECTOR; GENETICS; HYPERLIPIDEMIA; HYPERLIPOPROTEINEMIA TYPE 2; MOUSE;

ANIMALS; DEPENDOVIRUS; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; HYPERLIPIDEMIAS; HYPERLIPOPROTEINEMIA TYPE II; MICE; RECEPTORS, LDL;

EID: 0034264614     PISSN: 15250016     EISSN: None     Source Type: Journal    
DOI: 10.1006/mthe.2000.0122     Document Type: Article

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