Extreme thrombocytosis in response to PEG-ADA: Early therapeutic and risk indicator

Clinical Pediatrics

Volumn 39, Issue 3, 2000, Pages 183-186

  Marwaha, Vijay Rai ^a   Italia, Dinaz Homi ^a   Esper, Frank ^a   Hostoffer, Robert W ^b,c  

^a CASE WESTERN RESERVE UNIVERSITY SCHOOL OF MEDICINE   (United States)

^b CASE WESTERN RESERVE UNIVERSITY   (United States)

^c University Suburban Health Center   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ADENOSINE DEAMINASE; PEGADEMASE;

ARTICLE; CASE REPORT; CLINICAL FEATURE; COMBINED IMMUNODEFICIENCY; DIAGNOSTIC PROCEDURE; DISEASE COURSE; ENZYME DEFICIENCY; FEMALE; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMAN; INFANT; THROMBOCYTOSIS; TREATMENT OUTCOME;

EID: 0034069531     PISSN: 00099228     EISSN: None     Source Type: Journal    
DOI: 10.1177/000992280003900309     Document Type: Article

References (9)

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4. Hershfield MS, Buckley RH, Greenberg ML, et al. Treatment of adenosine deaminase deficiency with polyethylene glycol-modified adenosine deaminase. N Engl J Med. 1987;316: 589-596.
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7. Hirschhorn R. Inherited enzyme deficiencies and immunodificiency: adenosine deaminase (ADA) and purine nucleoside phosphorylase (PNP) deficiencies. Clin Immunol Immunopathol. 1986;40:157-165.
8. Hershfield MS. PEG-ADA replacement therapy for adenosine deaminase deficiency: an update for 8.5 years. Clin Immunol Immunopathol. 1995;76:S228-S232.
9. Hershfield MS, Chaffee S, Sorensen RU. Enzyme replacement therapy with polyethylene glycol-adenosine deaminase deficiency: overview and case reports of three patients, including two now receiving gene therapy. Pediatr Res. 1993;33:S42-S47.