'Supercharged cells' for delivery of recombinant human iduronate-2-sulfatase

Molecular Genetics and Metabolism

Volumn 70, Issue 3, 2000, Pages 170-178

  Pan, Dao ^a   Jonsson, Jon J ^a   Braun, Stephen E ^a   McIvor, R Scott ^a   Whitley, Chester B ^a  

^a UNIVERSITY OF MINNESOTA MEDICAL SCHOOL   (United States)

Author keywords

Cross correction; Gene therapy; Glycosaminoglycan; Hunter syndrome; Mucopolysaccharidosis; Retrovirus; Super charged cells

Indexed keywords

GLYCOSAMINOGLYCAN; IDURONATE 2 SULFATASE; RECOMBINANT ENZYME; VIRUS VECTOR;

ARTICLE; ENZYME ACTIVITY; GENE THERAPY; GENE TRANSFER; HUMAN; HUMAN CELL; HUNTER SYNDROME; LYMPHOCYTE; MUCOPOLYSACCHARIDOSIS; NONHUMAN; PRIORITY JOURNAL; RETROVIRUS; X CHROMOSOME LINKED DISORDER;

EID: 0033863202     PISSN: 10967192     EISSN: None     Source Type: Journal    
DOI: 10.1006/mgme.2000.3012     Document Type: Article

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