Comparative efficacy of dose regimens in enzyme replacement therapy of type I Gaucher disease

Blood Cells, Molecules, and Diseases

Volumn 26, Issue 4, 2000, Pages 285-290

  Altarescu, G ^a   Schiffmann, R ^a   Parker, C C ^a   Moore, D F ^a   Kreps, C ^a   Brady, R O ^a   Barton, N W ^a  

^a NATIONAL INSTITUTE OF NEUROLOGICAL DISORDERS AND STROKE   (United States)

Author keywords

Enzyme replacement therapy; Gaucher type I; Macrophage targeted glucocerebrosidase; Metabolic disease; Treatment

Indexed keywords

ACID PHOSPHATASE; ALGLUCERASE; GLUCOSYLCERAMIDASE; HEMOGLOBIN;

ADOLESCENT; ADULT; AGED; ARTICLE; CLINICAL TRIAL; CONTROLLED CLINICAL TRIAL; CONTROLLED STUDY; DISEASE ACTIVITY; DOSE RESPONSE; DRUG EFFICACY; ENZYME REPLACEMENT; FEMALE; GAUCHER DISEASE; HEMOGLOBIN DETERMINATION; HUMAN; LIVER WEIGHT; MACROPHAGE; MALE; MAXIMUM ALLOWABLE CONCENTRATION; PRIORITY JOURNAL; SCHOOL CHILD; SPLEEN WEIGHT; THROMBOCYTE COUNT; TREATMENT OUTCOME;

EID: 0033730925     PISSN: 10799796     EISSN: None     Source Type: Journal    
DOI: 10.1006/bcmd.2000.0310     Document Type: Article

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