Inosine15.1 hammerhead ribozymes for targeting the transthyretin-30 mutation

Biochemical and Biophysical Research Communications

Volumn 260, Issue 2, 1999, Pages 313-317

  Pröpsting, Marcus J ^a   Blaschke, Martina ^a   Haas, Regina E ^a   Genschel, Janine ^a   Hedrich, H J ^a   Manns, Michael P ^a   Schmidt, Hartmut H J ^a  

^a HANNOVER MEDICAL SCHOOL   (Germany)

Author keywords

Hammerhead; Inosine; Mutation; Ribozyme; Therapy; Transthyretin

Indexed keywords

ADENOSINE; INOSINE; MESSENGER RNA; METHIONINE; MUTANT PROTEIN; NUCLEASE; PREALBUMIN; RIBOZYME; VALINE;

AMINO ACID SEQUENCE; AMINO ACID SUBSTITUTION; AMYLOIDOSIS; ARTICLE; CONTROLLED STUDY; GENE MUTATION; GENE TARGETING; GENE THERAPY; ISOTOPE LABELING; PRIORITY JOURNAL; RNA CLEAVAGE; CHEMISTRY; CONFORMATION; GENETICS; HYDROLYSIS; METABOLISM; MUTATION;

HYDROLYSIS; INOSINE; MUTATION; NUCLEIC ACID CONFORMATION; PREALBUMIN; RNA, CATALYTIC; RNA, MESSENGER;

EID: 0033526663     PISSN: 0006291X     EISSN: None     Source Type: Journal    
DOI: 10.1006/bbrc.1999.0906     Document Type: Article

References (26)

1. Benson M., Uemichi T. Amyloid: Int. J. Exp. Clin. Invest. 3:1996;44-56.
2. Sipe J. D. Crit. Rev. Clin. Lab. Sci. 31:1994;325-354.
3. McCutchen S. L., Lai Z., Miroy G. J., Kelly J. W., Colon W. Biochemistry. 34:1995;13527-13536.
4. Felding P., Fex G., Westermark P., Olofsson B. O., Pitkanen P., Benson L. Scand. J. Immunol. 21:1985;133-140.
5. Neuromuscul. Disord. 6:1996;S6-S96.
6. Lewis W. D., Skinner M., Simms R. W., Jones L. A., Cohen A. S., Jenkins R. L. Clin. Transplant. 8:1994;107-110.
7. Benson M. Scriver C., Beaudet A., Sly W., Nolle D. The Metabolic Basis of Inherited Diseases. 1995;4159-4191 McGraw-Hill, New York.
8. Schmidt H. H.-J., Nashan B., Pröpsting M. J., Nakazato M., Flemming P., Kubicka S., Böker K., Pichlmayr R., Manns M. P. J. Hepatol. 30:1998;293-298.
9. Scott W. G., Klug A. Trends Biochem. Sci. 21:1996;220-224.
10. Ohkawa J., Koguma T., Kohda T., Taira K. J. Biochem. (Tokyo). 118:1995;251-258.
11. Phylactou L. A., Tsipouras P., Kilpatrick M. W. Biochem. Biophys. Res. Commun. 249:1998;804-810.
12. Birikh K. R., Heaton P. A., Eckstein F. Eur. J. Biochem. 245:1997;1-16.
13. Cameron F. H., Jennings P. A. Proc. Natl. Acad. Sci. USA. 86:1989;9139-9143.
14. Cotten M., Birnstiel M. L. EMBO J. 8:1989;3861-3866.
15. Heidenreich O., Eckstein F. J. Biol. Chem. 267:1992;1904-1909.
16. Paolella G., Sproat B. S., Lamond A. I. EMBO J. 11:1992;1913-1919.
17. Lamond A. I., Sproat B. S. FEBS Lett. 325:1993;123-127.
18. Sproat B. S., Lamond A. I., Garcia R. G., Beijer B., Pieles U., Douglas M., Bohmann K., Carmo-Fonseco M., Weston S., O'Loughlin S. Nucleic Acids Symp. Ser. 1991;59-62.
19. Pieken W. A., Olsen D. B., Benseler F., Aurup H., Eckstein F. Science. 253:1991;314-317.
20. Williams D. M., Pieken W. A., Eckstein F. Proc. Natl. Acad. Sci. USA. 89:1992;918-921.
21. Heidenreich O., Benseler F., Fahrenholz A., Eckstein F. J. Biol. Chem. 269:1994;2131-2138.
22. Leirdal M., Sioud M. Biochem. Biophys. Res. Commun. 250:1998;171-174.
23. Beigelman L., McSwiggen J. A., Draper K. G., Gonzalez C., Jensen K., Karpeisky A. M., Modak A. S., Matulic-Adamic J., DiRenzo A. B., Haeberli P. J. Biol. Chem. 270:1995;25702-25708.
24. Ludwig J., Blaschke M., Sproat B. S. Nucleic Acids Res. 26:1998;2279-2285.
25. Lyngstadaas S. P., Risnes S., Sproat B. S., Thrane P. S., Prydz H. P. EMBO J. 14:1995;5224-5229.
26. Heidenreich O., Pieken W., Eckstein F. FASEB J. 7:1993;90-96.