-
1
-
-
0029914677
-
Gene transfer into the mouse retina mediated by an adeno-associated viral vector
-
Ali RR, Reichel MB, Thrasher AJ, Levinsky RJ, Kinnon C, Kanuga N, Hunt DM, Bhattacharya SS (1996) Gene transfer into the mouse retina mediated by an adeno-associated viral vector. Hum Mol Genet 5: 591-594
-
(1996)
Hum Mol Genet
, vol.5
, pp. 591-594
-
-
Ali, R.R.1
Reichel, M.B.2
Thrasher, A.J.3
Levinsky, R.J.4
Kinnon, C.5
Kanuga, N.6
Hunt, D.M.7
Bhattacharya, S.S.8
-
2
-
-
0031985556
-
Adeno-associated virus gene transfer to mouse retina
-
Ali RR, Reichel MB, De Alwis M, Kanuga N, Kinnon C, Levinsky RJ, Hunt DM, Bhattacharya SS, Thrasher AJ (1998) Adeno-associated virus gene transfer to mouse retina. Hum Gene Ther 9: 81-86
-
(1998)
Hum Gene Ther
, vol.9
, pp. 81-86
-
-
Ali, R.R.1
Reichel, M.B.2
De Alwis, M.3
Kanuga, N.4
Kinnon, C.5
Levinsky, R.J.6
Hunt, D.M.7
Bhattacharya, S.S.8
Thrasher, A.J.9
-
3
-
-
0023081188
-
Adeno-associated viruses: An update
-
Berns KI, Bohenzky RA (1987) Adeno-associated viruses: an update. Adv Virus Res 32: 243-306
-
(1987)
Adv Virus Res
, vol.32
, pp. 243-306
-
-
Berns, K.I.1
Bohenzky, R.A.2
-
4
-
-
0024536789
-
The β-globin dominant control region activates homologous and heterologous promoters in a tissue-specific manner
-
Blom van Assendelft G, Hanscombe O, Grosveld F, Greaves DR (1989) The β-globin dominant control region activates homologous and heterologous promoters in a tissue-specific manner. Cell 56: 969-977
-
(1989)
Cell
, vol.56
, pp. 969-977
-
-
Blom Van Assendelft, G.1
Hanscombe, O.2
Grosveld, F.3
Greaves, D.R.4
-
5
-
-
0028138645
-
Dissection of the locus control function located on the chicken lysozyme gene domain in transgenic mice
-
Bonifer C, Yannoutsos N, Kruger G, Grosveld F, Sippel AE (1994) Dissection of the locus control function located on the chicken lysozyme gene domain in transgenic mice. Nucleic Acids Res 22: 4202-4210
-
(1994)
Nucleic Acids Res
, vol.22
, pp. 4202-4210
-
-
Bonifer, C.1
Yannoutsos, N.2
Kruger, G.3
Grosveld, F.4
Sippel, A.E.5
-
6
-
-
0029097707
-
Modulation of enhancer-promoter interactions by insulators in the Drosophila embryo
-
Cai H, Levine M (1995) Modulation of enhancer-promoter interactions by insulators in the Drosophila embryo. Nature 376: 533-536
-
(1995)
Nature
, vol.376
, pp. 533-536
-
-
Cai, H.1
Levine, M.2
-
7
-
-
0027254748
-
A 5′ element of the chicken β-globin domain serves as an insulator in human erythroid cells and protects against position effect in Drosophila
-
Chung JH, Whiteley M, Felsenfeld G (1993) A 5′ element of the chicken β-globin domain serves as an insulator in human erythroid cells and protects against position effect in Drosophila. Cell 74: 505-514
-
(1993)
Cell
, vol.74
, pp. 505-514
-
-
Chung, J.H.1
Whiteley, M.2
Felsenfeld, G.3
-
9
-
-
0025101148
-
Definition of the minimal requirements within the human β-globin gene and the dominant control region for high level expression
-
Collis P, Antoniou M, Grosveld F (1990) Definition of the minimal requirements within the human β-globin gene and the dominant control region for high level expression. EMBO J 9: 233-240
-
(1990)
EMBO J
, vol.9
, pp. 233-240
-
-
Collis, P.1
Antoniou, M.2
Grosveld, F.3
-
10
-
-
0023113052
-
Regulated expression of a complete human β-globin gene encoded by a transmissible retrovirus vector
-
Cone RD, Weber-Benarous A, Baorto D, Mulligan RC (1987) Regulated expression of a complete human β-globin gene encoded by a transmissible retrovirus vector. Mol Cell Biol 7: 887-897
-
(1987)
Mol Cell Biol
, vol.7
, pp. 887-897
-
-
Cone, R.D.1
Weber-Benarous, A.2
Baorto, D.3
Mulligan, R.C.4
-
11
-
-
0029166448
-
Chromatin insulators. Keeping enhancers under control
-
Corces VG (1995) Chromatin insulators. Keeping enhancers under control. Nature 376: 462-463
-
(1995)
Nature
, vol.376
, pp. 462-463
-
-
Corces, V.G.1
-
12
-
-
0023864651
-
Lineage-specific expression of a human β-globin gene in murine bone marrow transplant recipients reconstituted with retrovirus-transduced stem cells
-
Dzierzak EA, Papayannopoulou T, Mulligan RC (1988) Lineage-specific expression of a human β-globin gene in murine bone marrow transplant recipients reconstituted with retrovirus-transduced stem cells. Nature 331: 35-41
-
(1988)
Nature
, vol.331
, pp. 35-41
-
-
Dzierzak, E.A.1
Papayannopoulou, T.2
Mulligan, R.C.3
-
13
-
-
0029145011
-
Regulated high-level human β-globin gene expression in erythroid cells following recombinant adeno-associated virus-mediated gene transfer
-
Einerhand MP, Antoniou M, Zolotukhin S, Muzyczka N, Berns KI, Grosveld F, Valerio D (1995) Regulated high-level human β-globin gene expression in erythroid cells following recombinant adeno-associated virus-mediated gene transfer. Gene Ther 2: 336-343
-
(1995)
Gene Ther
, vol.2
, pp. 336-343
-
-
Einerhand, M.P.1
Antoniou, M.2
Zolotukhin, S.3
Muzyczka, N.4
Berns, K.I.5
Grosveld, F.6
Valerio, D.7
-
14
-
-
0026500372
-
Bone marrow transplantation for severe sickle cell anaemia
-
Ferster A, De Valck C, Azzi N, Fondu P, Toppet M, Sariban E (1992) Bone marrow transplantation for severe sickle cell anaemia. Br J Haematol 80: 102-105
-
(1992)
Br J Haematol
, vol.80
, pp. 102-105
-
-
Ferster, A.1
De Valck, C.2
Azzi, N.3
Fondu, P.4
Toppet, M.5
Sariban, E.6
-
15
-
-
0031058024
-
Recombinant adeno-associated virus for muscle directed gene therapy
-
Fisher KJ, Jooss K, Alston J, Yang Y, Haecker SE, High K, Pathak R, Raper SE, Wilson JM (1997) Recombinant adeno-associated virus for muscle directed gene therapy. Nature Med 3: 306-312
-
(1997)
Nature Med
, vol.3
, pp. 306-312
-
-
Fisher, K.J.1
Jooss, K.2
Alston, J.3
Yang, Y.4
Haecker, S.E.5
High, K.6
Pathak, R.7
Raper, S.E.8
Wilson, J.M.9
-
16
-
-
0026738877
-
DNa position-specific repression of transcription by a Drosophila zinc finger protein
-
Geyer PK, Corces VG (1992) DNA position-specific repression of transcription by a Drosophila zinc finger protein. Genes Dev 6: 1865-1873
-
(1992)
Genes Dev
, vol.6
, pp. 1865-1873
-
-
Geyer, P.K.1
Corces, V.G.2
-
17
-
-
0027992020
-
Recombinant adeno-associated virus-mediated gene transfer into hematopoietic progenitor cells
-
Goodman S, Xiao X, Donahue RE, Moulton A, Miller J, Walsh C, Young NS, Samulski RJ, Nienhuis AW (1994) Recombinant adeno-associated virus-mediated gene transfer into hematopoietic progenitor cells. Blood 84: 1492-1500
-
(1994)
Blood
, vol.84
, pp. 1492-1500
-
-
Goodman, S.1
Xiao, X.2
Donahue, R.E.3
Moulton, A.4
Miller, J.5
Walsh, C.6
Young, N.S.7
Samulski, R.J.8
Nienhuis, A.W.9
-
18
-
-
0023663887
-
Position-independent, high-level expression of the human β-globin gene in transgenic mice
-
Grosveld F, van Assendelft GB, Greaves DR, Kollias G (1987) Position-independent, high-level expression of the human β-globin gene in transgenic mice. Cell 51: 975-985
-
(1987)
Cell
, vol.51
, pp. 975-985
-
-
Grosveld, F.1
Van Assendelft, G.B.2
Greaves, D.R.3
Kollias, G.4
-
19
-
-
0029939592
-
The β-globin locus control region enhances transcription of but does not confer position-independent expression onto the lacZ gene in transgenic mice
-
Guy LG, Kothary R, DeRepentigny Y, Delvoye N, Ellis J, Wall L (1996) The β-globin locus control region enhances transcription of but does not confer position-independent expression onto the lacZ gene in transgenic mice. EMBO J 15: 3713-3721
-
(1996)
EMBO J
, vol.15
, pp. 3713-3721
-
-
Guy, L.G.1
Kothary, R.2
DeRepentigny, Y.3
Delvoye, N.4
Ellis, J.5
Wall, L.6
-
20
-
-
0030721660
-
Position effects in mice carrying a lacZ transgene in ciz with the β-globin LCR can be explained by a graded model
-
Guy LG, Kothary R, Wall L (1997) Position effects in mice carrying a lacZ transgene in ciz with the β-globin LCR can be explained by a graded model. Nucleic Acids Res 25: 4400-4407
-
(1997)
Nucleic Acids Res
, vol.25
, pp. 4400-4407
-
-
Guy, L.G.1
Kothary, R.2
Wall, L.3
-
21
-
-
0017689608
-
Establishment and characterization of KB cell lines latently infected with adeno-associated virus type 1
-
Handa H, Shiroki K, Shimojo H (1977) Establishment and characterization of KB cell lines latently infected with adeno-associated virus type 1. Virology 82: 84-92
-
(1977)
Virology
, vol.82
, pp. 84-92
-
-
Handa, H.1
Shiroki, K.2
Shimojo, H.3
-
22
-
-
0026100193
-
Repression of hsp70 heat shock gene transcription by the suppressor of hairy-wing protein of Drosophila melanogaster
-
Holdridge C, Dorsett D (1991) Repression of hsp70 heat shock gene transcription by the suppressor of hairy-wing protein of Drosophila melanogaster. Mol Cell Biol 11: 1894-1900
-
(1991)
Mol Cell Biol
, vol.11
, pp. 1894-1900
-
-
Holdridge, C.1
Dorsett, D.2
-
23
-
-
0028988485
-
Position-independent transgene expression mediated by boundary elements from the apolipoprotein B chromatin domain
-
Kalos M, Fournier RE (1995) Position-independent transgene expression mediated by boundary elements from the apolipoprotein B chromatin domain. Mol Cell Biol 15: 198-207
-
(1995)
Mol Cell Biol
, vol.15
, pp. 198-207
-
-
Kalos, M.1
Fournier, R.E.2
-
24
-
-
0029836472
-
Recombinant adeno-associated virus (AAV-CFTR) vectors do not integrate in a site-specific fashion in an immortalized epithelial cell line
-
Kearns WG, Afione SA, Fulmer SB, Pang MC, Erikson D, Egan M, Landrum MJ, Flotte TR, Cutting GR (1996) Recombinant adeno-associated virus (AAV-CFTR) vectors do not integrate in a site-specific fashion in an immortalized epithelial cell line. Gene Ther 3: 748-755
-
(1996)
Gene Ther
, vol.3
, pp. 748-755
-
-
Kearns, W.G.1
Afione, S.A.2
Fulmer, S.B.3
Pang, M.C.4
Erikson, D.5
Egan, M.6
Landrum, M.J.7
Flotte, T.R.8
Cutting, G.R.9
-
25
-
-
0026027982
-
A position-effect assay for boundaries of higher order chromosomal domains
-
Kellum R, Schedl P (1991) A position-effect assay for boundaries of higher order chromosomal domains. Cell 64: 941-950
-
(1991)
Cell
, vol.64
, pp. 941-950
-
-
Kellum, R.1
Schedl, P.2
-
26
-
-
0026711089
-
A group of ses elements function as domain boundaries in an enhancer- Blocking assay
-
Kellum R, Schedl P (1992) A group of ses elements function as domain boundaries in an enhancer- blocking assay. Mol Cell Biol 12: 2424-2431
-
(1992)
Mol Cell Biol
, vol.12
, pp. 2424-2431
-
-
Kellum, R.1
Schedl, P.2
-
27
-
-
0027092001
-
Characterization of a preferred site on human chromosome 19q for integration of adeno-associated virus DNa by non-homologous recombination
-
Kotin RM, Linden RM. Berns KI (1992) Characterization of a preferred site on human chromosome 19q for integration of adeno-associated virus DNA by non-homologous recombination. EMBO J 11: 5071-5078
-
(1992)
EMBO J
, vol.11
, pp. 5071-5078
-
-
Kotin, R.M.1
Linden, R.M.2
Berns, K.I.3
-
28
-
-
0028303758
-
Mutagenesis of retroviral vectors transducing human β-globin gene and β-globin locus control region derivatives results in stable transmission of an active transcriptional structure
-
Leboulch P, Huang GM, Humphries RK, Oh YH, Eaves CJ, Tuan DY, London IM (1994) Mutagenesis of retroviral vectors transducing human β-globin gene and β-globin locus control region derivatives results in stable transmission of an active transcriptional structure. EMBO J 13: 3065-3076
-
(1994)
EMBO J
, vol.13
, pp. 3065-3076
-
-
Leboulch, P.1
Huang, G.M.2
Humphries, R.K.3
Oh, Y.H.4
Eaves, C.J.5
Tuan, D.Y.6
London, I.M.7
-
29
-
-
0020466344
-
+ thalassemia
-
+ thalassemia. N Engl J Med 307: 1469-1475
-
(1982)
N Engl J Med
, vol.307
, pp. 1469-1475
-
-
Ley, T.J.1
DeSimone, J.2
Anagnou, N.P.3
Keller, G.H.4
Humphries, R.K.5
Turner, P.H.6
Young, N.S.7
Keller, P.8
Nienhuis, A.W.9
-
30
-
-
0023692635
-
Delineation of individual human chromosomes in metaphase and interphase cells by in situ suppression hybridization using recombinant DNA libraries
-
Lichter P, Cremer T, Borden J, Manuelidis L, Ward DC (1988) Delineation of individual human chromosomes in metaphase and interphase cells by in situ suppression hybridization using recombinant DNA libraries. Hum Genet 80: 224-234
-
(1988)
Hum Genet
, vol.80
, pp. 224-234
-
-
Lichter, P.1
Cremer, T.2
Borden, J.3
Manuelidis, L.4
Ward, D.C.5
-
31
-
-
0027998844
-
Hypersensitive site 5 of the human β locus control region functions as a chromatin insulator
-
Li Q, Stamatoyannopoulos G (1994) Hypersensitive site 5 of the human β locus control region functions as a chromatin insulator. Blood 84: 1399-1401
-
(1994)
Blood
, vol.84
, pp. 1399-1401
-
-
Li, Q.1
Stamatoyannopoulos, G.2
-
32
-
-
0025070260
-
Bone marrow transplantation in patients with thalassemia
-
Lucarelli G, Galimberti M, Polchi P, Angelucci E, Baronciani D, Giardini C, Politi P, Durazzi SM, Muretto P, Albertini F (1990) Bone marrow transplantation in patients with thalassemia. N Engl J Med 322: 417-421
-
(1990)
N Engl J Med
, vol.322
, pp. 417-421
-
-
Lucarelli, G.1
Galimberti, M.2
Polchi, P.3
Angelucci, E.4
Baronciani, D.5
Giardini, C.6
Politi, P.7
Durazzi, S.M.8
Muretto, P.9
Albertini, F.10
-
33
-
-
0031058475
-
Recombinant adeno-associated virus mediates a high level of gene transfer but less efficient integration in the K562 human hematopoietic cell line
-
Malik P, McQuiston SA, Yu XJ, Pepper KA, Krall WJ, Podsakoff GM, Kurtzman GJ, Kohn DB (1997) Recombinant adeno-associated virus mediates a high level of gene transfer but less efficient integration in the K562 human hematopoietic cell line. J Virol 71: 1776-1783
-
(1997)
J Virol
, vol.71
, pp. 1776-1783
-
-
Malik, P.1
McQuiston, S.A.2
Yu, X.J.3
Pepper, K.A.4
Krall, W.J.5
Podsakoff, G.M.6
Kurtzman, G.J.7
Kohn, D.B.8
-
34
-
-
0030003480
-
Differential and persistent expression patterns of CNS gene transfer by an adeno-associated virus (AAV) vector
-
McCown TJ, Xiao X, Li J, Breese GR, Samulski RJ (1996) Differential and persistent expression patterns of CNS gene transfer by an adeno-associated virus (AAV) vector. Brain Res 713: 99-107
-
(1996)
Brain Res
, vol.713
, pp. 99-107
-
-
McCown, T.J.1
Xiao, X.2
Li, J.3
Breese, G.R.4
Samulski, R.J.5
-
35
-
-
0027317003
-
Single-copy transduction and expression of human γ-globin in K562 erythroleukemia cells using recombinant adeno-associated virus vectors: The effect of mutations in NF-E2 and GATA-1 binding motifs within the hypersensitivity site 2 enhancer
-
Miller JL, Walsh CE, Ney PA, Samulski RJ, Nienhuis AW (1993) Single-copy transduction and expression of human γ-globin in K562 erythroleukemia cells using recombinant adeno-associated virus vectors: The effect of mutations in NF-E2 and GATA-1 binding motifs within the hypersensitivity site 2 enhancer. Blood 82: 1900-1906
-
(1993)
Blood
, vol.82
, pp. 1900-1906
-
-
Miller, J.L.1
Walsh, C.E.2
Ney, P.A.3
Samulski, R.J.4
Nienhuis, A.W.5
-
36
-
-
0025291510
-
Tandem AP-1-binding sites within the human β-globin dominant control region function as an inducible enhancer in erythroid cells
-
Ney PA. Sorrentino BP, McDonagh KT, Nienhuis AW (1990) Tandem AP-1-binding sites within the human β-globin dominant control region function as an inducible enhancer in erythroid cells. Genes Dev 4: 993-1006
-
(1990)
Genes Dev
, vol.4
, pp. 993-1006
-
-
Ney, P.A.1
Sorrentino, B.P.2
McDonagh, K.T.3
Nienhuis, A.W.4
-
37
-
-
0025295890
-
High-level β-globin expression after retroviral transfer of locus activation region-containing human β-globin gene derivatives into murine erythroleukemia cells
-
Novak U, Harris EA, Forrester W, Groudine M, Gelinas R (1990) High-level β-globin expression after retroviral transfer of locus activation region-containing human β-globin gene derivatives into murine erythroleukemia cells. Proc Natl Acad Sci USA 87: 3386-3390
-
(1990)
Proc Natl Acad Sci USA
, vol.87
, pp. 3386-3390
-
-
Novak, U.1
Harris, E.A.2
Forrester, W.3
Groudine, M.4
Gelinas, R.5
-
38
-
-
0025292742
-
The β-globin dominant control region: Hypersensitive site 2
-
Philipsen S, Talbot D, Fraser P, Grosveld F (1990) The β-globin dominant control region: Hypersensitive site 2. EMBO J 9: 2159-2167
-
(1990)
EMBO J
, vol.9
, pp. 2159-2167
-
-
Philipsen, S.1
Talbot, D.2
Fraser, P.3
Grosveld, F.4
-
39
-
-
0030979112
-
Adeno-associated virus type 2-mediated transduction of murine hcmatopoietic cells with long-term repopulating ability and sustained expression of a human globin gene in vivo
-
Ponnazhagan S, Yoder MC, Srivastava A (1997) Adeno-associated virus type 2-mediated transduction of murine hcmatopoietic cells with long-term repopulating ability and sustained expression of a human globin gene in vivo. J Virol 74: 3098-3104
-
(1997)
J Virol
, vol.74
, pp. 3098-3104
-
-
Ponnazhagan, S.1
Yoder, M.C.2
Srivastava, A.3
-
40
-
-
0025819055
-
Hypersensitive site 4 of the human β-globin locus control region
-
Pruzma S, Hanscombe O, Whyatt D, Grosveld F, Philipsen S (1991) Hypersensitive site 4 of the human β-globin locus control region. Nucleic Acids Res 19: 1413-1419
-
(1991)
Nucleic Acids Res
, vol.19
, pp. 1413-1419
-
-
Pruzma, S.1
Hanscombe, O.2
Whyatt, D.3
Grosveld, F.4
Philipsen, S.5
-
41
-
-
0025310642
-
Developmental regulation of topoisomerase II sites and DNase I- Hypersensitive sites in the chicken β-globin locus
-
Reitman M, Felsenfeld G (1990) Developmental regulation of topoisomerase II sites and DNase I- hypersensitive sites in the chicken β-globin locus. Mol Cell Biol 10: 2774-2786
-
(1990)
Mol Cell Biol
, vol.10
, pp. 2774-2786
-
-
Reitman, M.1
Felsenfeld, G.2
-
42
-
-
0029242185
-
AAV as a viral vector for human gene therapy. Generation of recombinant virus
-
Rolling F, Samulski RJ (1995) AAV as a viral vector for human gene therapy. Generation of recombinant virus. Mol Biotechnol 3: 9-15
-
(1995)
Mol Biotechnol
, vol.3
, pp. 9-15
-
-
Rolling, F.1
Samulski, R.J.2
-
43
-
-
0027402685
-
The su(Hw) protein insulates expression of the Drosophila melanogaster white gene from chromosomal position-effects
-
Roseman RR, Pirrotta V, Geyer PK (1993) The su(Hw) protein insulates expression of the Drosophila melanogaster white gene from chromosomal position-effects. EMBO J 12: 435-442
-
(1993)
EMBO J
, vol.12
, pp. 435-442
-
-
Roseman, R.R.1
Pirrotta, V.2
Geyer, P.K.3
-
44
-
-
0031897270
-
Human gene targeting by viral vectors
-
Russell DW, Hirata RK (1998) Human gene targeting by viral vectors. Nat Genet 18: 325-330
-
(1998)
Nat Genet
, vol.18
, pp. 325-330
-
-
Russell, D.W.1
Hirata, R.K.2
-
45
-
-
0024635998
-
A single erythroid-specific DNase I super-hyper-sensitive site activates high levels of human β-globin gene expression in transgenic mice
-
Ryan TM, Behringer RR, Martin NC, Townes TM, Palmiter RD, Brinster RL (1989) A single erythroid-specific DNase I super-hyper-sensitive site activates high levels of human β-globin gene expression in transgenic mice. Genes Dev 3: 314-323
-
(1989)
Genes Dev
, vol.3
, pp. 314-323
-
-
Ryan, T.M.1
Behringer, R.R.2
Martin, N.C.3
Townes, T.M.4
Palmiter, R.D.5
Brinster, R.L.6
-
46
-
-
0029084785
-
Generation of a high-titer retroviral vector capable of expressing high levels of the human β-globin gene
-
Sadelain M, Wang CH, Antoniou M, Grosveld F, Mulligan RC (1995) Generation of a high-titer retroviral vector capable of expressing high levels of the human β-globin gene. Proc Natl Acad Sci USA 92: 6728-6732
-
(1995)
Proc Natl Acad Sci USA
, vol.92
, pp. 6728-6732
-
-
Sadelain, M.1
Wang, C.H.2
Antoniou, M.3
Grosveld, F.4
Mulligan, R.C.5
-
48
-
-
0026070440
-
Targeted integration of adeno-associated virus (AAV) into human chromosome 19
-
Samulski RJ, Zhu X, Xiao X, Brook JD, Housman DE, Epstein N, Hunter LA (1991) Targeted integration of adeno-associated virus (AAV) into human chromosome 19. EMBO J 10: 3941-3950
-
(1991)
EMBO J
, vol.10
, pp. 3941-3950
-
-
Samulski, R.J.1
Zhu, X.2
Xiao, X.3
Brook, J.D.4
Housman, D.E.5
Epstein, N.6
Hunter, L.A.7
-
49
-
-
0029174794
-
Effects of the su(Hw) insulator protein on the expression of the divergently transcribed Drosophila yolk protein genes
-
Scott KS, Geyer PK (1995) Effects of the su(Hw) insulator protein on the expression of the divergently transcribed Drosophila yolk protein genes. EMBO J 14: 6258-6267
-
(1995)
EMBO J
, vol.14
, pp. 6258-6267
-
-
Scott, K.S.1
Geyer, P.K.2
-
50
-
-
0030997346
-
Persistent and therapeutic concentrations of human factor IX in mice after hepatic gene transfer of recombinant AAV vectors
-
Snyder RO, Miao CH, Patijn GA, Spratt SK, Danos O, Nagy D, Gown AM, Winther B, Meuse L, Cohen LK, Thompson AR, Kay MA (1997a) Persistent and therapeutic concentrations of human factor IX in mice after hepatic gene transfer of recombinant AAV vectors. Nat Genet 16: 270-276
-
(1997)
Nat Genet
, vol.16
, pp. 270-276
-
-
Snyder, R.O.1
Miao, C.H.2
Patijn, G.A.3
Spratt, S.K.4
Danos, O.5
Nagy, D.6
Gown, A.M.7
Winther, B.8
Meuse, L.9
Cohen, L.K.10
Thompson, A.R.11
Kay, M.A.12
-
51
-
-
0030671462
-
Efficient and stable adeno-associated virus-mediated transduction in the skeletal muscle of adult immunocompetent mice
-
Snyder RO, Spratt SK, Lagarde C, Bohl D, Kaspar B, Sloan B, Cohen LK, Danos O (1997b) Efficient and stable adeno-associated virus-mediated transduction in the skeletal muscle of adult immunocompetent mice. Hum Gene Ther 8: 1891-1900
-
(1997)
Hum Gene Ther
, vol.8
, pp. 1891-1900
-
-
Snyder, R.O.1
Spratt, S.K.2
Lagarde, C.3
Bohl, D.4
Kaspar, B.5
Sloan, B.6
Cohen, L.K.7
Danos, O.8
-
52
-
-
0024506821
-
A dominant control region from the human β-globin locus conferring integration site-independent gene expression
-
Talbot D, Collis P, Antoniou M, Vidal M, Grosveld F, Greaves DR (1989) A dominant control region from the human β-globin locus conferring integration site-independent gene expression. Nature 338: 352-355
-
(1989)
Nature
, vol.338
, pp. 352-355
-
-
Talbot, D.1
Collis, P.2
Antoniou, M.3
Vidal, M.4
Grosveld, F.5
Greaves, D.R.6
-
53
-
-
0025365230
-
Detailed analysis of the site 3 region of the human β-globin dominant control region
-
Talbot D, Philipsen S, Fraser P, Grosveld F (1990) Detailed analysis of the site 3 region of the human β-globin dominant control region. EMBO J 9: 2169-2177
-
(1990)
EMBO J
, vol.9
, pp. 2169-2177
-
-
Talbot, D.1
Philipsen, S.2
Fraser, P.3
Grosveld, F.4
-
54
-
-
0026660060
-
Regulated high level expression of a human γ-globin gene introduced into erythroid cells by an adeno-associated virus vector
-
Walsh CE, Liu JM, Xiao X, Young NS, Nienhuis AW, Samulski RJ (1992) Regulated high level expression of a human γ-globin gene introduced into erythroid cells by an adeno-associated virus vector. Proc Natl Acad Sci USA 89: 7257-7261
-
(1992)
Proc Natl Acad Sci USA
, vol.89
, pp. 7257-7261
-
-
Walsh, C.E.1
Liu, J.M.2
Xiao, X.3
Young, N.S.4
Nienhuis, A.W.5
Samulski, R.J.6
-
56
-
-
0021833690
-
Prevention of cardiac disease by subcutaneous deferoxamine in patients with thalassemia major
-
Wolfe L, Olivieri N, Sallan D, Colan S, Rose V, Propper R, Freedman MH, Nathan DG (1985) Prevention of cardiac disease by subcutaneous deferoxamine in patients with thalassemia major. N Engl J Med 312: 1600-1603
-
(1985)
N Engl J Med
, vol.312
, pp. 1600-1603
-
-
Wolfe, L.1
Olivieri, N.2
Sallan, D.3
Colan, S.4
Rose, V.5
Propper, R.6
Freedman, M.H.7
Nathan, D.G.8
-
57
-
-
0030928619
-
Gene therapy - Promises, problems and prospects
-
Verma IM, Somia N (1997) Gene therapy - promises, problems and prospects. Nature 389: 239-242
-
(1997)
Nature
, vol.389
, pp. 239-242
-
-
Verma, I.M.1
Somia, N.2
|