Merosin-deficient congenital muscular dystrophy: Partial genetic correction in two mouse models

Journal of Clinical Investigation

Volumn 102, Issue 4, 1998, Pages 844-852

  Kuang, Wen ^a,b   Xu, Hong ^a   Vachon, Pierre H ^a,d   Liu, Ling ^a,b   Loechel, Frosty ^c   Wewer, Ulla M ^c   Engvall, Eva ^a,b  

^a BURNHAM INSTITUTE   (United States)

^b STOCKHOLM UNIVERSITY   (Sweden)

^c UNIVERSITY OF COPENHAGEN   (Denmark)

^d UNIVERSITÉ DE SHERBROOKE   (Canada)

Author keywords

Gene targeting; Gene therapy; Merosin; Muscular dystrophy; Transgenic mice

Indexed keywords

LAMININ; MEROSIN;

ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CONTROLLED STUDY; GENE EXPRESSION; GENE MUTATION; GENE STRUCTURE; GENE TARGETING; GENE THERAPY; MOUSE; MUSCULAR DYSTROPHY; NONHUMAN; PRIORITY JOURNAL; PROTEIN EXPRESSION; TRANSGENIC MOUSE;

EID: 0032528845     PISSN: 00219738     EISSN: None     Source Type: Journal    
DOI: 10.1172/JCI3705     Document Type: Article

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