-
1
-
-
0028790442
-
Molecular medicine: Muscle-based gene therapy
-
Blau H.M., Springer M.L. Molecular medicine: muscle-based gene therapy. New Engl. J. Med. 333:1995;1554-1556.
-
(1995)
New Engl. J. Med.
, vol.333
, pp. 1554-1556
-
-
Blau, H.M.1
Springer, M.L.2
-
2
-
-
0030117962
-
Muscle-based gene therapy: Realistic possibilities for the future
-
Svensson E.C., Tripathy S.K., Leiden J.M. Muscle-based gene therapy: realistic possibilities for the future. Mol. Med. Today. 2:1996;166-172.
-
(1996)
Mol. Med. Today
, vol.2
, pp. 166-172
-
-
Svensson, E.C.1
Tripathy, S.K.2
Leiden, J.M.3
-
3
-
-
0023614188
-
Dystrophin: The protein product of the Duchenne muscular dystrophy locus
-
Hoffman E.P., Brown R.H. Jr., Kunkel L.M. Dystrophin: the protein product of the Duchenne muscular dystrophy locus. Cell. 51:1987;919-928.
-
(1987)
Cell
, vol.51
, pp. 919-928
-
-
Hoffman, E.P.1
Brown R.H., Jr.2
Kunkel, L.M.3
-
4
-
-
0024300196
-
Immuno-electron microscopic localization of dystrophin in myofibers
-
Watkins S.C., Hoffman E.P., Slayter H.S., Kunkel L.M. Immuno-electron microscopic localization of dystrophin in myofibers. Nature. 333:1988;863-866.
-
(1988)
Nature
, vol.333
, pp. 863-866
-
-
Watkins, S.C.1
Hoffman, E.P.2
Slayter, H.S.3
Kunkel, L.M.4
-
5
-
-
0025887093
-
Human dystrophin expression in mdx mice after intramuscular injection of DNA constructs
-
Acsadi G.et al. Human dystrophin expression in mdx mice after intramuscular injection of DNA constructs. Nature. 352:1991;815-818.
-
(1991)
Nature
, vol.352
, pp. 815-818
-
-
Acsadi, G.1
-
6
-
-
0026570486
-
Retroviral-mediated transfer of a dystrophin minigene into mdx mouse myoblasts in vitro
-
Dunckley M.G.et al. Retroviral-mediated transfer of a dystrophin minigene into mdx mouse myoblasts in vitro. FEbs Lett. 296:1992;128-134.
-
(1992)
FEbs Lett.
, vol.296
, pp. 128-134
-
-
Dunckley, M.G.1
-
7
-
-
0027408847
-
Efficient adenovirus-mediated transfer of a human mini-dystrophin gene to skeletal muscle of mdx mice
-
Ragot T.et al. Efficient adenovirus-mediated transfer of a human mini-dystrophin gene to skeletal muscle of mdx mice. Nature. 361:1993;647-650.
-
(1993)
Nature
, vol.361
, pp. 647-650
-
-
Ragot, T.1
-
8
-
-
0027362435
-
Long-term correction of mouse dystrophic degeneration by adenovirus-mediated transfer of a mini-dystrophin gene
-
Vincent N.et al. Long-term correction of mouse dystrophic degeneration by adenovirus-mediated transfer of a mini-dystrophin gene. Nat. Genet. 5:1993;130-134.
-
(1993)
Nat. Genet.
, vol.5
, pp. 130-134
-
-
Vincent, N.1
-
9
-
-
0024540879
-
Conversion of mdx myofibers from dystrophin negative to positive by injection of normal myoblasts
-
Partridge T.A.et al. Conversion of mdx myofibers from dystrophin negative to positive by injection of normal myoblasts. Nature. 337:1989;176-179.
-
(1989)
Nature
, vol.337
, pp. 176-179
-
-
Partridge, T.A.1
-
10
-
-
0027269957
-
Myoblast transfer in Duchenne muscular dystrophy
-
Karpati G.et al. Myoblast transfer in Duchenne muscular dystrophy. Ann. Neurol. 34:1993;8-17.
-
(1993)
Ann. Neurol.
, vol.34
, pp. 8-17
-
-
Karpati, G.1
-
11
-
-
0027166930
-
Results of a triple blind clinical study of myoblast transplantations without immunosuppressive treatment in young boys with Duchenne muscular dystrophy
-
Tremblay J.P.et al. Results of a triple blind clinical study of myoblast transplantations without immunosuppressive treatment in young boys with Duchenne muscular dystrophy. Cell Transplant. 2:1993;99-112.
-
(1993)
Cell Transplant.
, vol.2
, pp. 99-112
-
-
Tremblay, J.P.1
-
13
-
-
0027933842
-
Gene transfer into skeletal muscles by isogenic myoblasts
-
Huard J.et al. Gene transfer into skeletal muscles by isogenic myoblasts. Hum. Gene Ther. 5:1994;949-958.
-
(1994)
Hum. Gene Ther.
, vol.5
, pp. 949-958
-
-
Huard, J.1
-
14
-
-
0029129834
-
Myoblast transfer in the treatment of Duchenne's muscular dystrophy
-
Mendell J.R.et al. Myoblast transfer in the treatment of Duchenne's muscular dystrophy. New Engl. J. Med. 333:1995;832-838.
-
(1995)
New Engl. J. Med.
, vol.333
, pp. 832-838
-
-
Mendell, J.R.1
-
15
-
-
0030865245
-
The fate of individual myoblasts after transplantation into muscles of DMD patients
-
Gussoni E., Blau H.M., Kunkel L.M. The fate of individual myoblasts after transplantation into muscles of DMD patients. Nat. Med. 3:1997;970-977.
-
(1997)
Nat. Med.
, vol.3
, pp. 970-977
-
-
Gussoni, E.1
Blau, H.M.2
Kunkel, L.M.3
-
16
-
-
0030899172
-
Control of inflammatory damage by anti-LFA-1: Increase success of myoblast transplantation
-
Guerrette B.et al. Control of inflammatory damage by anti-LFA-1: increase success of myoblast transplantation. Cell Transplant. 6:1997;101-107.
-
(1997)
Cell Transplant.
, vol.6
, pp. 101-107
-
-
Guerrette, B.1
-
17
-
-
0026922764
-
Long-term persistence of plasmid DNA and foreign gene expression in mouse muscle
-
Wolff J.A.et al. Long-term persistence of plasmid DNA and foreign gene expression in mouse muscle. Hum. Mol. Genet. 1:1992;363-369.
-
(1992)
Hum. Mol. Genet.
, vol.1
, pp. 363-369
-
-
Wolff, J.A.1
-
18
-
-
0027713222
-
Plasmid DNA is superior to viral vectors for direct gene transfer into adult mouse skeletal muscle
-
Davis H.L.et al. Plasmid DNA is superior to viral vectors for direct gene transfer into adult mouse skeletal muscle. Hum. Gene Ther. 4:1993;733-740.
-
(1993)
Hum. Gene Ther.
, vol.4
, pp. 733-740
-
-
Davis, H.L.1
-
19
-
-
0027283418
-
Direct gene transfer into skeletal muscle in vivo: Factors affecting efficiency of transfer and stability of expression
-
Davis H.L., Whalen R.G., Demeneix B.A. Direct gene transfer into skeletal muscle in vivo: factors affecting efficiency of transfer and stability of expression. Hum. Gene Ther. 4:1993;151-159.
-
(1993)
Hum. Gene Ther.
, vol.4
, pp. 151-159
-
-
Davis, H.L.1
Whalen, R.G.2
Demeneix, B.A.3
-
20
-
-
0030749978
-
Spatial-temporal patterns of gene expression in mouse skeletal muscle after injection of LacZ plasmid DNA
-
Doh S.G.et al. Spatial-temporal patterns of gene expression in mouse skeletal muscle after injection of LacZ plasmid DNA. Gene Ther. 4:1997;648-663.
-
(1997)
Gene Ther.
, vol.4
, pp. 648-663
-
-
Doh, S.G.1
-
21
-
-
0029982279
-
Condensation of plasmid DNA with polylysine improves liposome-mediated gene transfer into established and primary muscle cells
-
Vitiello L.et al. Condensation of plasmid DNA with polylysine improves liposome-mediated gene transfer into established and primary muscle cells. Gene Ther. 3:1996;396-404.
-
(1996)
Gene Ther.
, vol.3
, pp. 396-404
-
-
Vitiello, L.1
-
22
-
-
0030794156
-
Selection and use of ligands for receptor-mediated gene delivery to myogenic cells
-
Feero W.G.et al. Selection and use of ligands for receptor-mediated gene delivery to myogenic cells. Gene Ther. 4:1997;664-674.
-
(1997)
Gene Ther.
, vol.4
, pp. 664-674
-
-
Feero, W.G.1
-
23
-
-
0026349206
-
Systemic delivery of recombinant proteins by genetically modified myoblasts
-
Barr E., Leiden J.M. Systemic delivery of recombinant proteins by genetically modified myoblasts. Science. 254:1991;1507-1509.
-
(1991)
Science
, vol.254
, pp. 1507-1509
-
-
Barr, E.1
Leiden, J.M.2
-
24
-
-
0026335995
-
Systemic delivery of human growth hormone by injection of genetically engineered myoblasts
-
Dhawan J.et al. Systemic delivery of human growth hormone by injection of genetically engineered myoblasts. Science. 254:1991;1509-1512.
-
(1991)
Science
, vol.254
, pp. 1509-1512
-
-
Dhawan, J.1
-
25
-
-
0027787054
-
Retroviral-mediated gene transfer into human primary myogenic cells lead to expression in muscle fibers in vivo
-
Salvatori G.et al. Retroviral-mediated gene transfer into human primary myogenic cells lead to expression in muscle fibers in vivo. Hum. Gene Ther. 4:1993;713-723.
-
(1993)
Hum. Gene Ther.
, vol.4
, pp. 713-723
-
-
Salvatori, G.1
-
26
-
-
0025279872
-
Gene transfer by retrovirus vectors occurs only in cells that are actively replicating at the time of infection
-
Miller D.G., Adam M.A., Miller A.D. Gene transfer by retrovirus vectors occurs only in cells that are actively replicating at the time of infection. Mol. Cell. Biol. 10:1990;4239-4242.
-
(1990)
Mol. Cell. Biol.
, vol.10
, pp. 4239-4242
-
-
Miller, D.G.1
Adam, M.A.2
Miller, A.D.3
-
27
-
-
0028346944
-
A differential efficiency of adenovirus-mediated in vivo gene transfer into skeletal muscle cells of different maturity
-
Acsadi G.et al. A differential efficiency of adenovirus-mediated in vivo gene transfer into skeletal muscle cells of different maturity. Hum. Mol. Genet. 3:1994;579-584.
-
(1994)
Hum. Mol. Genet.
, vol.3
, pp. 579-584
-
-
Acsadi, G.1
-
29
-
-
0030066219
-
Dystrophin expression in muscles of mdx mice after adenovirus-mediated in vivo gene transfer
-
Acsadi G.et al. Dystrophin expression in muscles of mdx mice after adenovirus-mediated in vivo gene transfer. Hum. Gene Ther. 7:1996;129-140.
-
(1996)
Hum. Gene Ther.
, vol.7
, pp. 129-140
-
-
Acsadi, G.1
-
30
-
-
0029943155
-
A new adenoviral vector: Replacement of all viral coding sequences with 28 kb of DNA independently expressing both full-length dystrophin and β-galactosidase
-
Kochanek S.et al. A new adenoviral vector: replacement of all viral coding sequences with 28 kb of DNA independently expressing both full-length dystrophin and β-galactosidase. Proc. Natl. Acad. Sci. U. S. A. 93:1996;5731-5736.
-
(1996)
Proc. Natl. Acad. Sci. U. S. A.
, vol.93
, pp. 5731-5736
-
-
Kochanek, S.1
-
31
-
-
0030016358
-
Encapsidated adenovirus minichromosomes allow delivery and expression of a 14 kb dystrophin cDNA to muscle cells
-
Kumar-Singh R., Chamberlain J.S. Encapsidated adenovirus minichromosomes allow delivery and expression of a 14 kb dystrophin cDNA to muscle cells. Hum. Mol. Genet. 5:1996;913-921.
-
(1996)
Hum. Mol. Genet.
, vol.5
, pp. 913-921
-
-
Kumar-Singh, R.1
Chamberlain, J.S.2
-
32
-
-
0029962474
-
In vivo expression of full-length human dystrophin from adenoviral vectors deleted of all viral genes
-
Haecker S.E.et al. In vivo expression of full-length human dystrophin from adenoviral vectors deleted of all viral genes. Hum. Gene Ther. 7:1996;1907-1914.
-
(1996)
Hum. Gene Ther.
, vol.7
, pp. 1907-1914
-
-
Haecker, S.E.1
-
33
-
-
0029797726
-
The basal lamina is a physical barrier to herpes simplex virus-mediated gene delivery to mature muscle fibers
-
Huard J.et al. The basal lamina is a physical barrier to herpes simplex virus-mediated gene delivery to mature muscle fibers. J. Virol. 70:1996;8117-8123.
-
(1996)
J. Virol.
, vol.70
, pp. 8117-8123
-
-
Huard, J.1
-
34
-
-
0030896088
-
LacZ gene transfer to skeletal muscle using a replication-defective herpes simplex virus type 1 mutant vector
-
Huard J.et al. LacZ gene transfer to skeletal muscle using a replication-defective herpes simplex virus type 1 mutant vector. Hum. Gene Ther. 8:1997;439-452.
-
(1997)
Hum. Gene Ther.
, vol.8
, pp. 439-452
-
-
Huard, J.1
-
35
-
-
0030824160
-
Gene transfer to muscle using herpes simplex virus-based vectors
-
Huard J.et al. Gene transfer to muscle using herpes simplex virus-based vectors. Neuromusc. Disord. 7:1997;1-15.
-
(1997)
Neuromusc. Disord.
, vol.7
, pp. 1-15
-
-
Huard, J.1
-
36
-
-
0029843596
-
Efficient long-term gene transfer into muscle tissue of immunocompetent mice by adeno-associated virus vector
-
Xiao X., Li J., Samulski R.J. Efficient long-term gene transfer into muscle tissue of immunocompetent mice by adeno-associated virus vector. J. Virol. 70:1996;8098-8108.
-
(1996)
J. Virol.
, vol.70
, pp. 8098-8108
-
-
Xiao, X.1
Li, J.2
Samulski, R.J.3
-
37
-
-
0031058024
-
Recombinant adeno-associated virus for muscle directed gene therapy
-
Fisher K.J.et al. Recombinant adeno-associated virus for muscle directed gene therapy. Nat. Med. 3:1997;306-312.
-
(1997)
Nat. Med.
, vol.3
, pp. 306-312
-
-
Fisher, K.J.1
-
38
-
-
0026545146
-
Cytotoxicity of a replication-defective mutant of herpes simplex virus type 1
-
Johnson P.A.et al. Cytotoxicity of a replication-defective mutant of herpes simplex virus type 1. J. Virol. 66:1992;2952-2965.
-
(1992)
J. Virol.
, vol.66
, pp. 2952-2965
-
-
Johnson, P.A.1
-
39
-
-
0028807696
-
FK506 immunosuppression to control the immune reactions triggered by first-generation adenovirus-mediated gene transfer
-
Vilquin J.T.et al. FK506 immunosuppression to control the immune reactions triggered by first-generation adenovirus-mediated gene transfer. Hum. Gene Ther. 6:1995;1391-1401.
-
(1995)
Hum. Gene Ther.
, vol.6
, pp. 1391-1401
-
-
Vilquin, J.T.1
-
40
-
-
0029790327
-
Prevention of immune reactions triggered by first-generation adenoviral vectors by monoclonal antibodies and CTLA4Ig
-
Guerette B.et al. Prevention of immune reactions triggered by first-generation adenoviral vectors by monoclonal antibodies and CTLA4Ig. Hum. Gene Ther. 7:1996;1455-1463.
-
(1996)
Hum. Gene Ther.
, vol.7
, pp. 1455-1463
-
-
Guerette, B.1
-
41
-
-
0031049699
-
Persistence in muscle of an adenoviral vector that lacks all viral genes
-
Chen H.H.et al. Persistence in muscle of an adenoviral vector that lacks all viral genes. Proc. Natl. Acad. Sci. U. S. A. 94:1997;1645-1650.
-
(1997)
Proc. Natl. Acad. Sci. U. S. A.
, vol.94
, pp. 1645-1650
-
-
Chen, H.H.1
-
42
-
-
0007531886
-
Viral gene delivery to skeletal muscle: Insights on maturation-dependent loss of fiber infectivity for adenovirus and herpes simplex type 1 viral vectors
-
Feero W.G.et al. Viral gene delivery to skeletal muscle: insights on maturation-dependent loss of fiber infectivity for adenovirus and herpes simplex type 1 viral vectors. Hum. Gene Ther. 8:1997;371-380.
-
(1997)
Hum. Gene Ther.
, vol.8
, pp. 371-380
-
-
Feero, W.G.1
-
43
-
-
0028500191
-
Cultured human myoblasts and myotubes show markedly different transducibility by replication-defective adenovirus recombinants
-
Acsadi G.et al. Cultured human myoblasts and myotubes show markedly different transducibility by replication-defective adenovirus recombinants. Gene Ther. 1:1994;338-340.
-
(1994)
Gene Ther.
, vol.1
, pp. 338-340
-
-
Acsadi, G.1
-
44
-
-
0029858682
-
Adenovirus targeted to heparan-containing receptors increases its gene delivery efficiency to multiple cell types
-
Wickham T.J.et al. Adenovirus targeted to heparan-containing receptors increases its gene delivery efficiency to multiple cell types. Nat. Biotechnol. 14:1996;1570-1573.
-
(1996)
Nat. Biotechnol.
, vol.14
, pp. 1570-1573
-
-
Wickham, T.J.1
-
45
-
-
0025353203
-
Assembly of basement membranes
-
Yurchenco P.D. Assembly of basement membranes. Ann. New York Acad. Sci. 580:1990;195-213.
-
(1990)
Ann. New York Acad. Sci.
, vol.580
, pp. 195-213
-
-
Yurchenco, P.D.1
-
46
-
-
0028334735
-
Defective muscle basement membrane and lack of M-laminin in the dystrophic dy/dy mouse
-
Xu H.et al. Defective muscle basement membrane and lack of M-laminin in the dystrophic dy/dy mouse. Proc. Natl. Acad. Sci. U. S. A. 91:1994;5572-5576.
-
(1994)
Proc. Natl. Acad. Sci. U. S. A.
, vol.91
, pp. 5572-5576
-
-
Xu, H.1
-
47
-
-
0028385738
-
Pharmacological enhancement of in vivo foreign gene expression in muscle
-
Danko I.et al. Pharmacological enhancement of in vivo foreign gene expression in muscle. Gene Ther. 1:1994;114-121.
-
(1994)
Gene Ther.
, vol.1
, pp. 114-121
-
-
Danko, I.1
-
48
-
-
0027937512
-
Gene transfer in regenerating muscle
-
Vitadello M.et al. Gene transfer in regenerating muscle. Hum. Gene Ther. 5:1994;11-18.
-
(1994)
Hum. Gene Ther.
, vol.5
, pp. 11-18
-
-
Vitadello, M.1
-
49
-
-
0030925358
-
Myoblast mediated ex vivo gene transfer to mature muscle
-
Booth D.K.et al. Myoblast mediated ex vivo gene transfer to mature muscle. Tissue Eng. 3:1997;125-133.
-
(1997)
Tissue Eng.
, vol.3
, pp. 125-133
-
-
Booth, D.K.1
-
50
-
-
6844257545
-
Ex vivo gene transfer using adenovirus mediated full-length dystrophin delivery to mature dystrophic muscles
-
Floyd S.S.et al. Ex vivo gene transfer using adenovirus mediated full-length dystrophin delivery to mature dystrophic muscles. Gene Ther. 5:1998;19-30.
-
(1998)
Gene Ther.
, vol.5
, pp. 19-30
-
-
Floyd, S.S.1
|