Characterization of an MDR1 retroviral bicistronic vector for correction of X-linked severe combined immunodeficiency

Gene Therapy

Volumn 5, Issue 5, 1998, Pages 671-676

  Kleiman, S E ^a,b   Pastan, I ^a   Puck, J M ^c   Gottesman, M M ^a,d  

^a NATIONAL CANCER INSTITUTE   (United States)

^b TEL AVIV SOURASKY MEDICAL CENTER   (Israel)

^c NATIONAL HUMAN GENOME RESEARCH INSTITUTE   (United States)

^d NATIONAL INSTITUTES OF HEALTH   (United States)

Author keywords

Gene transfer; MDR1; Retroviral vectors; XSCID

Indexed keywords

COMPLEMENTARY DNA; GLYCOPROTEIN P; INTERLEUKIN 2 RECEPTOR; MEMBRANE PROTEIN; MONOCLONAL ANTIBODY; PHOSPHATE;

ANIMAL CELL; ARTICLE; B LYMPHOCYTE; COMBINED IMMUNODEFICIENCY; CONTROLLED STUDY; DNA TRANSFECTION; EXPRESSION VECTOR; FIBROBLAST; FLUORESCENCE ACTIVATED CELL SORTER; GENE TRANSFER; GENETIC TRANSDUCTION; IMMUNOBLOTTING; LYMPHOID CELL LINE; MOUSE; NONHUMAN; PRIORITY JOURNAL; PROTEIN EXPRESSION; RIBOSOME; RNA TRANSLATION; X CHROMOSOME LINKAGE;

ANIMALIA;

EID: 0031803563     PISSN: 09697128     EISSN: None     Source Type: Journal    
DOI: 10.1038/sj.gt.3300651     Document Type: Article

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