Designing clinical trials to study rare disease treatment

Drug Information Journal

Volumn 32, Issue 4, 1998, Pages 957-960

  Haffner, M E ^a  

^a CENTER FOR DRUG EVALUATION AND RESEARCH   (United States)

Author keywords

Clinical trial design; Office of Orphan Products Development; Orphan Drug Act; Orphan drugs; Rare diseases

Indexed keywords

ADENOSINE DEAMINASE; ERYTHROPOIETIN; GANCICLOVIR; LORENZO OIL; ORPHAN DRUG; PLACEBO;

ADRENOLEUKODYSTROPHY; CHRONIC KIDNEY FAILURE; CLINICAL PROTOCOL; CLINICAL TRIAL; CONTROLLED CLINICAL TRIAL; CROSSOVER PROCEDURE; DRUG LEGISLATION; DRUG THERAPY; DRUG WITHDRAWAL; ENZYME DEFICIENCY; FOOD AND DRUG ADMINISTRATION; HUMAN; INTRAVITREAL DRUG ADMINISTRATION; PRIORITY JOURNAL; RANDOMIZED CONTROLLED TRIAL; RETINITIS; REVIEW;

EID: 0031741255     PISSN: 00928615     EISSN: None     Source Type: Journal    
DOI: 10.1177/009286159803200413     Document Type: Review

References (0)