Low-dose high-frequency enzyme replacement therapy prevents fractures without complete suppression of painful bone crises in patients with severe juvenile onset type I Gaucher disease: Commentary

Blood Cells, Molecules, and Diseases

Volumn 24, Issue 3, 1998, Pages 303-308

  Zimran, A ^a   Cohen, I J ^a   Zaizov, R ^a  

^a SHAARE ZEDEK MEDICAL CENTER   (Israel)

Author keywords

[No Author keywords available]

Indexed keywords

IMIGLUCERASE; NARCOTIC AGENT; NONSTEROID ANTIINFLAMMATORY AGENT; PREDNISONE;

AVASCULAR NECROSIS; BONE PAIN; BONE RADIOGRAPHY; ENZYME REPLACEMENT; FRACTURE; GAUCHER DISEASE; HUMAN; NOTE; ORAL DRUG ADMINISTRATION; PRIORITY JOURNAL;

EID: 0031728421     PISSN: 10799796     EISSN: None     Source Type: Journal    
DOI: 10.1006/bcmd.1998.0196     Document Type: Editorial

References (17)

1. E RB McCabe BA Fine MS Globus Gaucher disease - Current issues in diagnosis and treatment J Am Med Assoc 275 1996 548 553
2. ML Figueroa BE Rosenbloom AC Kay A less costly regimen of alglucerase to treat Gaucher's disease N Engl J Med 327 1992 1632 1636
3. A Zimran D Elstein R Kannai Low-dose enzyme replacement therapy for Gaucher's disease: effects of age, sex, genotype, and clinical features on response to treatment Am J Med 97 1994 3 13
4. NW Barton RO Brady JM Dambrosia Replacement therapy for inherited enzyme deficiency: macrophage-targeted glucocerebrosidase for Gaucher's disease N Engl J Med 324 1991 1464 1470
5. DI Rosenthal SH Doppelt HJ Mankin Enzyme replacement therapy for Gaucher disease: skeletal responses to macrophage-targeted glucocerebrosidase Pediatrics 96 1995 629 637
6. D Elstein I Hadas-Halpern M Itzchaki Effect of low-dose enzyme replacement therapy on bones in Gaucher disease patients with severe skeletal involvement Blood Cells Mol Dis 22 1996 100 108
7. NW Barton RO Brady JM Dambrosia Dose dependent responses to macrophage-targeted glucocerebrosidase in a child with Gaucher disease J Pediatr 120 1992 277 280
8. GM Pastores AR Sibille GA Grabowski Enzyme therapy in Gaucher disease type 1: dosage, efficacy and adverse effects in 33 patients treated for 6 to 24 months Blood 82 1993 408 416
9. E Sidransky EI Ginns JA Westman Pathological fractures may occur in Gaucher patients receiving enzyme replacement therapy Am J Hematol 47 1994 247 249
10. E Beutler A Demina K Laubscher The clinical course of treated and untreated Gaucher disease. A study of 45 patients Blood Cells Mol Dis 21 1995 86 108
11. IJ Cohen K Katz L Kornreich Low-dose high-frequency enzyme replacement therapy prevents fractures without complete suppression of painful bone crises in patients with severe juvenile onset type I Gaucher disease Blood Cells Mol Dis 24 1998 296 302
12. R Zaizov A Frisch IJ Cohen Lower-dose, high-frequency enzyme replacement therapy in children with type I Gaucher disease: experience at the Schneider Children's Medical Center of Israel Semin Hematol 32 1995 39 44
13. PK Mistry A Abrahamov A practical approach to diagnosis and management of Gaucher's disease Bailliére's Clin Haematol 10 1997 817 838
14. Z Yosipovitch K Katz Bone crisis in Gaucher disease - an update Is J Med Sci 26 1990 593 595
15. A Zimran D Elstein R Schiffmann Outcome of partial splenectomy in type I Gaucher disease J Pediatr 126 1995 596 597
16. D Elstein M Itzchaki HJ Mankin Skeletal involvement in Gaucher disease Bailliére's Clin Haematol 10 1997 793 816
17. D Elstein A Abrahamov I Hadas-Halpern Low-dose low-frequency imiglucerase as a starting regimen of enzyme replacement therapy for patients with Gaucher disease Q J Med 91 1998 483 488