Regression with bounded outcome score: Evaluation of power by bootstrap and simulation in a chronic myelogenous leukaemia clinical trial

Statistics in Medicine

Volumn 17, Issue 17, 1998, Pages 1909-1922

  Tsodikov, A ^a,b   Hasenclever, D ^b   Loeffler, M ^b  

^a UNIVERSITY OF UTAH   (United States)

^b UNIVERSITY OF LEIPZIG   (Germany)

Author keywords

[No Author keywords available]

Indexed keywords

CYTARABINE; HYDROXYUREA; INTERFERON;

ARTICLE; CHRONIC MYELOID LEUKEMIA; CLINICAL TRIAL; CYTOGENETICS; HUMAN; PHILADELPHIA 1 CHROMOSOME; REGRESSION ANALYSIS; SIMULATION; STATISTICAL MODEL; TREATMENT OUTCOME;

ANTINEOPLASTIC COMBINED CHEMOTHERAPY PROTOCOLS; BONE MARROW TRANSPLANTATION; COMBINED MODALITY THERAPY; CYTARABINE; HUMANS; HYDROXYUREA; INTERFERONS; LEUKEMIA, MYELOID, CHRONIC; LEUKEMIA, MYELOID, PHILADELPHIA-POSITIVE; MODELS, STATISTICAL; ODDS RATIO; OUTCOME AND PROCESS ASSESSMENT (HEALTH CARE); REGRESSION ANALYSIS; REMISSION INDUCTION;

EID: 0031670455     PISSN: 02776715     EISSN: None     Source Type: Journal    
DOI: 10.1002/(SICI)1097-0258(19980915)17:17<1909::AID-SIM890>3.0.CO;2-0     Document Type: Article

References (17)

1. Lesaffre, E., Scheys, I., Fröhlich, J. and Bluhmki, E. 'Calculation of power and sample size with bounded outcome scores', Statistics in Medicine, 12, 1063-1078 (1993).
2. Hamilton, M. A. and Collings, B. J. 'Determining the appropriate sample size for nonparametric tests for location shift', Technometrics, 33 (3), 327-337 (1991).
3. Lehmann, E. L. Nonparametrics, Statistical Methods Based on Ranks, Holden Day, San Francisco, 1975.
4. McCullagh, P. 'Regression models for ordinal data (with discussion)', Journal of the Royal Statistical Society, Series B, 42, 109-142 (1980).
5. Jones, D. R. and Whitehead, J. 'Sequential forms of the log rank and modified Wilcoxon tests for censored data', Biometrika, 66, 105-113 (1979); Correction Biometrika, 68, 576 (1981).
6. Hilton, J. 'The appropriateness of the Wilcoxon tests in ordinal data', Statistics in Medicine, 15, 631-645 (1996).
7. Whitehead, J. 'Sample size calculations of ordered categorical data', Statistics in Medicine, 12, 2257-2271 (1993).
8. Kantarjian, H., Deisseroth A., Kurzrock, R., Estrov, Z. Talpaz, M. 'Chronic myelogenous leukemia: a concise updata', Blood, 82, 691-703 (1993).
9. Grossman, A., Silver, R., Szatrowski, T., Gutfriend, A., Verma, R. and Benn, P. 'Densitometric analysis of Southern Blot autoradiographs and its application of monitoring patients with chronic myelogenous leukemia', Leukemia, 5, 540-547 (1991).
10. Kantarjian, H., Talpaz, M., Keating, M., Estey, E., O'Brien, S., Beran, M., McCredie K., Gutterman, J. and Freireich, E. 'Intensive chemotherapie induction followed by interferon-alpha maintenance in patients with Philadelphia chromosome-positive chronic myelogenous leukemia', Cancer, 1201-1206 (1991).
11. Ozer, H., George, S., Schiffer, C., Rao, K., Rao, N., Wurster-Hill, D., Arthur, D., Powell, B., Gottlieb, A., Peterson, B., Rai, K., Testa, J., LeBeau, M., Tantravahi, R. and Bloomfield, C. 'Prolonged subcutaneous administration of recombinant 2b Interferon in patients with previously untreated Philadelphia chromosome-positive chronic-phase chronic myelogenous leukemia: effect on remission duration and survival: Cancer and Leukemia Group B Study 8583', Blood, 82, 2975-2984 (1993).
12. Hinkley, D. 'Inference about the intersection in two-phase regression', Biometrika, 56, 495-504 (1969).
13. Stephens, D. 'Bayesian retrospective multiple-changepoint identification', Applied Statistics, 43, 159-178 (1994).
14. Matthews, J., Altman, D., Campbell, M. and Royston, P. 'Analysis of serial measurements in medical research', British Medical Journal, 300, 230-235 (1990).
15. Everitt, B. S. The Analysis of Contingency Tables, 2nd edn, Chapman and Hall, 1992.
16. Efron, B. and Tibshirani, R. J. An Introduction to the Bootstrap, Chapman and Hall, 1993.
17. Stone, M. 'An asymptotic equivalence of choice of model by cross-validation and Akaike's criterion', Journal of the Royal Statistical Society, Series B, 39, 44-47 (1997).