-
1
-
-
0025160084
-
Expression of human factor IX in rabbit hepatocytes by retrovirus-mediated gene transfer: Potential for gene therapy of hemophilia B
-
Armentano, D., Thompson, A. R., Darlington, G., and Woo, S. L. C. (1990). Expression of human factor IX in rabbit hepatocytes by retrovirus-mediated gene transfer: Potential for gene therapy of hemophilia B. Proc. Natl. Acad. Sci. USA 87, 6141-6145.
-
(1990)
Proc. Natl. Acad. Sci. USA
, vol.87
, pp. 6141-6145
-
-
Armentano, D.1
Thompson, A.R.2
Darlington, G.3
Woo, S.L.C.4
-
2
-
-
0025374283
-
Phenotypic correction of factor IX deficiency in skin fibroblasts of hemophilic dogs
-
Axelrod, J. H., Read, M. S., Brinkhous, K. M., and Verma, I. M. (1990). Phenotypic correction of factor IX deficiency in skin fibroblasts of hemophilic dogs. Proc. Natl. Acad. Sci. USA 87, 5173-5177.
-
(1990)
Proc. Natl. Acad. Sci. USA
, vol.87
, pp. 5173-5177
-
-
Axelrod, J.H.1
Read, M.S.2
Brinkhous, K.M.3
Verma, I.M.4
-
3
-
-
0003343116
-
Adeno-associated virus latent infection
-
(B. W. J. Mahy, A. C. Minson, and G. K. Darby, eds.) Cambridge University Press, Cambridge
-
Berns, K. I., Cheung, A., Ontrove, J., and Lewis, M. (1982). Adeno-associated virus latent infection. In "Virus Persistence" (B. W. J. Mahy, A. C. Minson, and G. K. Darby, eds.), p. 249. Cambridge University Press, Cambridge.
-
(1982)
Virus Persistence
, pp. 249
-
-
Berns, K.I.1
Cheung, A.2
Ontrove, J.3
Lewis, M.4
-
4
-
-
0029011723
-
Targeted disruption of the mouse factor VIII gene produces a model of haemophilia A
-
Bi, L., Lawler, A. M., Antonarakis, S. E., High, K. A., Gearhart, J. D., and Kazazian, H. H. (1995). Targeted disruption of the mouse factor VIII gene produces a model of haemophilia A. Nat. Genet. 10, 119-121.
-
(1995)
Nat. Genet.
, vol.10
, pp. 119-121
-
-
Bi, L.1
Lawler, A.M.2
Antonarakis, S.E.3
High, K.A.4
Gearhart, J.D.5
Kazazian, H.H.6
-
5
-
-
0028230779
-
Lack of expression from a retroviral vector after transduction of murine hematopoietic stem cells is associated with methylation in vivo
-
Challita, P., and Kohn, D. B. (1994). Lack of expression from a retroviral vector after transduction of murine hematopoietic stem cells is associated with methylation in vivo. Proc. Natl. Acad. Sci. U.S.A. 91, 2567-2571. (Pubitemid 24139388)
-
(1994)
Proceedings of the National Academy of Sciences of the United States of America
, vol.91
, Issue.7
, pp. 2567-2571
-
-
Challita, P.-M.1
Kohn, D.B.2
-
6
-
-
0029943193
-
Sustained expression of therapeutic levels of human factor VIII in mice
-
Connelly, S., Gardner, J. M., Lyons, R. M., McClelland, A., Kaleko, M. (1996). Sustained expression of therapeutic levels of human factor VIII in mice. Blood 87, 4671-4677. (Pubitemid 26162366)
-
(1996)
Blood
, vol.87
, Issue.11
, pp. 4671-4677
-
-
Connelly, S.1
Gardner, J.M.2
Lyons, R.M.3
McClelland, A.4
Kaleko, M.5
-
7
-
-
0026755818
-
High-efficiency receptor mediated delivery of small and large (48 kilobase) gene constructs using the endosome-disruption activity of defective or chemically inactivated adenovirus particles
-
Cotten, M., Wagner, E., Zatloukal, K., Phillips, S., and Birnstiel, M. L. (1992). High-efficiency receptor mediated delivery of small and large (48 kilobase) gene constructs using the endosome-disruption activity of defective or chemically inactivated adenovirus particles. Proc. Natl. Acad. Sci. USA 89, 6094-6098.
-
(1992)
Proc. Natl. Acad. Sci. USA
, vol.89
, pp. 6094-6098
-
-
Cotten, M.1
Wagner, E.2
Zatloukal, K.3
Phillips, S.4
Birnstiel, M.L.5
-
8
-
-
0001963451
-
Biology of adeno-associated virus
-
(K. I. Berns, ed.) Plenum Press, New York
-
Cukor, G., Blacklow, N. R., Hoggan, D., and Berns, K. I. (1984). Biology of adeno-associated virus. In "The Parvoviruses" (K. I. Berns, ed.), pp. 33-66. Plenum Press, New York.
-
(1984)
The Parvoviruses
, pp. 33-66
-
-
Cukor, G.1
Blacklow, N.R.2
Hoggan, D.3
Berns, K.I.4
-
9
-
-
0026486612
-
Gene therapy via primary myoblasts: Long-term expression of factor IX protein following transplantation in vivo
-
Dai, Y., Roman, M., Naviaux, R. K., and Verma, I. M. (1992). Gene therapy via primary myoblasts: Long-term expression of factor IX protein following transplantation in vivo. Proc. Natl. Acad. Sci. USA 89, 10892-10895.
-
(1992)
Proc. Natl. Acad. Sci. USA
, vol.89
, pp. 10892-10895
-
-
Dai, Y.1
Roman, M.2
Naviaux, R.K.3
Verma, I.M.4
-
10
-
-
0028934815
-
Cellular and humoral immune responses to adenoviral vectors containing factor IX gene: Tolerization of factor IX and vector antigens allows for long-term expression
-
Dai, Y., Schwarz, E. M., Gu, D., Zhang, W. W., Sarvetnick, N., and Verma, I. M. (1995). Cellular and humoral immune responses to adenoviral vectors containing factor IX gene: tolerization of factor IX and vector antigens allows for long-term expression. Proc. Natl. Acad. Sci. USA 92, 1401-1405.
-
(1995)
Proc. Natl. Acad. Sci. USA
, vol.92
, pp. 1401-1405
-
-
Dai, Y.1
Schwarz, E.M.2
Gu, D.3
Zhang, W.W.4
Sarvetnick, N.5
Verma, I.M.6
-
11
-
-
0026641562
-
Helper virus induced T cell lymphoma in nonhuman primates after retroviral mediated gene transfer
-
Donahue, R. E., Kessler, S. W., Bodine, D., McDonagh, K., Dunbar, C., Goodman, S., Agricola, B., Byrne, E., Raffeld, M., Moen, R., et al., (1992). Helper virus induced T cell lymphoma in nonhuman primates after retroviral mediated gene transfer. J. Exp. Med. 176(4), 1125-1135.
-
(1992)
J. Exp. Med.
, vol.176
, Issue.4
, pp. 1125-1135
-
-
Donahue, R.E.1
Kessler, S.W.2
Bodine, D.3
McDonagh, K.4
Dunbar, C.5
Goodman, S.6
Agricola, B.7
Byrne, E.8
Raffeld, M.9
Moen, R.10
-
12
-
-
0028842288
-
Gene therapy for hemophilia A: Production of therapeutic levels of human factor VIII in vitro in mice
-
Dwarki, V., Belloni, P., Nijjar, T., Smith, J., Couto, L., Rabier, M., Clift, S., Berns, A., and Cohen, L. K. (1995). Gene therapy for hemophilia A: Production of therapeutic levels of human factor VIII in vitro in mice. Proc. Natl. Acad. Sci. USA 92, 1023-1027.
-
(1995)
Proc. Natl. Acad. Sci. USA
, vol.92
, pp. 1023-1027
-
-
Dwarki, V.1
Belloni, P.2
Nijjar, T.3
Smith, J.4
Couto, L.5
Rabier, M.6
Clift, S.7
Berns, A.8
Cohen, L.K.9
-
13
-
-
79957637802
-
Characterization of recombinant human F. VIII
-
Eaton, D. L., Hass, P. E., Riddle, L., Mather, J., Wiebe, M., Gregory, T., Vehar, G. (1987). Characterization of recombinant human F. VIII. JBC 263, 1115-1118.
-
(1987)
JBC
, vol.263
, pp. 1115-1118
-
-
Eaton, D.L.1
Hass, P.E.2
Riddle, L.3
Mather, J.4
Wiebe, M.5
Gregory, T.6
Vehar, G.7
-
14
-
-
0028246338
-
Ablation of E2A in recombinant adenoviruses improves transgene persistence and decreases inflammatory response in mouse liver
-
DOI 10.1073/pnas.91.13.6196
-
Engelhardt, J. F., Ye, X., Doranz, B., and Wilson, J. M. (1994). Ablation of E2A in recombinant adenoviruses improves transgene persistence and decreases inflammatory response in mouse liver. Proc. Natl. Acad. Sci. USA 91, 6196-6200. (Pubitemid 24188310)
-
(1994)
Proceedings of the National Academy of Sciences of the United States of America
, vol.91
, Issue.13
, pp. 6196-6200
-
-
Engelhardt, J.F.1
Ye, X.2
Doranz, B.3
Wilson, J.M.4
-
15
-
-
0024805130
-
Canine hemophilia B resulting from a point mutation with unusual consequences
-
DOI 10.1073/pnas.86.24.10095
-
Evans, J. P., Brinkhous, K. M., Brayer, G. D., Reisner, H. M., and High, K. A. (1989a). Canine hemophilia B resulting from a point mutation with unusual consequences. Proc. Natl. Acad. Sci. USA 86, 10095-10099. (Pubitemid 20030783)
-
(1989)
Proceedings of the National Academy of Sciences of the United States of America
, vol.86
, Issue.24
, pp. 10095-10099
-
-
Evans, J.P.1
Brinkhous, K.M.2
Brayer, G.D.3
Reisner, H.M.4
High, K.A.5
-
16
-
-
0024313169
-
Molecular cloning of a cDNA encoding canine factor IX
-
Evans, J. P., Watzke, H. H., Ware, J. L., Stafford, D. W., and High, K. A. (1989b). Molecular cloning of a cDNA encoding canine factor IX. Blood 74(1), 207-212. (Pubitemid 19187430)
-
(1989)
Blood
, vol.74
, Issue.1
, pp. 207-212
-
-
Evans, J.P.1
Watzke, H.H.2
Ware, J.L.3
Stafford, D.W.4
High, K.A.5
-
17
-
-
0027484584
-
Stable in vivo expression of the cystic fibrosis transmembrane conductance regulator with an adeno-associated virus vector
-
DOI 10.1073/pnas.90.22.10613
-
Flotte, T. R., Afione, S. A., Conrad, C., McGrath, S. A., Solow, R., Oka, H., Zeitlin, P. L., Guggino, W B., and Carter, B. J. (1993). Stable in vivo expression of the cystic fibrosis transmembrane conductance regulator with an adeno-associated virus vector. Proc. Natl. Acad. Sci. USA 90, 10613-10617. (Pubitemid 23347092)
-
(1993)
Proceedings of the National Academy of Sciences of the United States of America
, vol.90
, Issue.22
, pp. 10613-10617
-
-
Flotte, T.R.1
Afione, S.A.2
Conrad, C.3
McGrath, S.A.4
Solow, R.5
Oka, H.6
Zeitlin, P.L.7
Guggino, W.B.8
Carter, B.J.9
-
18
-
-
0021750055
-
Characterization of the human factor VIII gene
-
DOI 10.1038/312326a0
-
Gitschier, J., Wood, W I., Goralka, T. M., Wion, K. L., Chen, E. Y., Eaton, D. H., Vehar, G. A., Capon, D. J., and Lawn, R. M. (1984). Characterization of the human factor VIII gene. Nature 312 (5992), 326-330. (Pubitemid 15209308)
-
(1984)
Nature
, vol.312
, Issue.5992
, pp. 326-330
-
-
Gitschier, J.1
Wood, W.I.2
Goralka, T.M.3
-
19
-
-
0024317522
-
A prospective study of human immunodeficiency virus type 1 infection and the development of AIDS in subjects with hemophilia
-
Goedert, J. J., Kessler, C. M., and Aledort, L. M. (1989). A prospective study of human immunodeficiency virus type 1 infection and the development of AIDS in subjects with hemophilia. N. Engl. J. Med. 321, 1141-1152.
-
(1989)
N. Engl. J. Med.
, vol.321
, pp. 1141-1152
-
-
Goedert, J.J.1
Kessler, C.M.2
Aledort, L.M.3
-
20
-
-
0021257303
-
Genetics of adeno-associated virus: Isolation and preliminary characterization of adeno-associated virus type 2 mutants
-
Hermonat, P. L., Labow, M. A., Wright, R., Berns, K. I., and Muzyzcka, N. (1984). Genetics of adeno-associated virus: Isolation and preliminary characterization of mutants of adeno-associated virus type 2. Virol. 51, 329-339. (Pubitemid 14091419)
-
(1984)
Journal of Virology
, vol.51
, Issue.2
, pp. 329-339
-
-
Hermonat, P.L.1
Labow, M.A.2
Wright, R.3
-
21
-
-
0026534020
-
Toward gene therapy in heamophilia A: Retrovirus-mediated transfer of a factor VIII gene into murine haematopoietic progenitor cells
-
Hoeben, R.C., Einerhand, M. P., Briet, E., van Ormondt, H., Valerio, D., and van der Eb, A. J. (1992). Toward gene therapy in heamophilia A: Retrovirus-mediated transfer of a factor VIII gene into murine haematopoietic progenitor cells. Thrombosis and Haemostasis 67(3), 341-345.
-
(1992)
Thrombosis and Haemostasis
, vol.67
, Issue.3
, pp. 341-345
-
-
Hoeben, R.C.1
Einerhand, M.P.2
Briet, E.3
Van Ormondt, H.4
Valerio, D.5
Van Der Eb, A.J.6
-
22
-
-
0025306056
-
Expression of functional factor VIII in primary human skin fibroblasts after retrovirus-mediated gene transfer
-
Hoeben, R. C., van der Jagt, R. C., Schoute, F., van Tilburg, N. H., Verbeet, M., Briet, E., van Ormondt, H., and van der Eb, A. (1990). Expression of functional factor VIII in primary human skin fibroblasts after retrovirus-mediated gene transfer. J. Biol. Chem. 265(13), 7318-7323.
-
(1990)
J. Biol. Chem.
, vol.265
, Issue.13
, pp. 7318-7323
-
-
Hoeben, R.C.1
Van Der Jagt, R.C.2
Schoute, F.3
Van Tilburg, N.H.4
Verbeet, M.5
Briet, E.6
Van Ormondt, H.7
Van Der Eb, A.8
-
23
-
-
0028169741
-
Long-term gene expression and phenotypic correction using adeno-associated virus vectors in the mammalian brain
-
DOI 10.1038/ng1094-148
-
Kaplitt, M. G., Leone, P., Samulski, R. J., Xiao, X., Pfaff, D. W., O'Malley, K. L., and During, M. J. (1994). Long-term gene expression and phenotypic correction using adeno-associated virus vectors in the mammalian brain. Nat. Genet. 8, 148-154. (Pubitemid 24308362)
-
(1994)
Nature Genetics
, vol.8
, Issue.2
, pp. 148-154
-
-
Kaplitt, M.G.1
Leone, P.2
Samulski, R.J.3
Xiao, X.4
Pfaff, D.W.5
O'Malley, K.L.6
During, M.J.7
-
24
-
-
0029113869
-
Long-term hepatic adenovirus-mediated gene expression in mice following CTLA4Ig administration
-
Kay, M. A., Holterman, A. X., Meuse, L., Gown, A., Ochs, H. D., Linsley, P. S., and Wilson, C. B. (1995). Long-term hepatic adenovirus-mediated gene expression in mice following CTLA4Ig administration. Nat. Genet. 11(2), 191-197.
-
(1995)
Nat. Genet.
, vol.11
, Issue.2
, pp. 191-197
-
-
Kay, M.A.1
Holterman, A.X.2
Meuse, L.3
Gown, A.4
Ochs, H.D.5
Linsley, P.S.6
Wilson, C.B.7
-
25
-
-
0028274169
-
In vivo hepatic gene therapy: Complete albeit transient correction of factor IX deficiency in hemophilia B dogs
-
Kay, M. A., Landen, C. N., Rothenberg, S. R., Taylor, L. A., Leland, F., Wiehle, S., Fang, B., Bellinger, D., Finegold, M., Thompson, A. R., et al., (1994). In vivo hepatic gene therapy: Complete albeit transient correction of factor IX deficiency in hemophilia B dogs. Proc. Natl. Acad. Sci. USA 91, 2353-2357. (Pubitemid 24092102)
-
(1994)
Proceedings of the National Academy of Sciences of the United States of America
, vol.91
, Issue.6
, pp. 2353-2357
-
-
Kay, M.A.1
Landen, C.N.2
Rothenberg, S.R.3
Taylor, L.A.4
Leland, F.5
Wiehle, S.6
Fang, B.7
Bellinger, D.8
Finegold, M.9
Thompson, A.R.10
Read, M.11
Brinkhous, K.M.12
Woo, S.L.C.13
-
26
-
-
0027686238
-
In vivo gene therapy of hemophilia B: Sustained partial correction in factor IX-deficient dogs
-
Kay, M. A., Rothenberg, S., Landen, C. N., Finegold, M., Thompson, A. R., Read, M. S., Brinkhous, K. M., and Woo, S. L. C. (1993). In vivo gene therapy of hemophilia B: Sustained partial correction in factor IX-deficient dogs. Science 262, 117-119.
-
(1993)
Science
, vol.262
, pp. 117-119
-
-
Kay, M.A.1
Rothenberg, S.2
Landen, C.N.3
Finegold, M.4
Thompson, A.R.5
Read, M.S.6
Brinkhous, K.M.7
Woo, S.L.C.8
-
27
-
-
0025214094
-
Site-specific integration by adeno-associated virus
-
Kotin, R. M., Siniscalco, R., Samulski, R. J., Zhu, X., Hunter, L., Laughlin, C. A., McLaughlin, S., Muzyczka, N., Rocchi, M., and Berns, K. I. (1990). Site-specific integration by adeno-associated virus. Proc. Natl. Acad. Sci. USA 87, 2211-2215.
-
(1990)
Proc. Natl. Acad. Sci. USA
, vol.87
, pp. 2211-2215
-
-
Kotin, R.M.1
Siniscalco, R.2
Samulski, R.J.3
Zhu, X.4
Hunter, L.5
Laughlin, C.A.6
McLaughlin, S.7
Muzyczka, N.8
Rocchi, M.9
Berns, K.I.10
-
29
-
-
0028076792
-
Efficient transfection of primary cells in a canine hemophilia B model using adenovirus-polylysine-DNA complexes
-
Lozier, J. N., Thompson, A. R., Hu, P.-C., Read, Brinkhous, K. M., High, K., and Curiel, D. T. (1994). Efficient transfection of primary cells in a canine hemophilia B model using adenovirus-polylysine-DNA complexes. Hum. Gene Ther. 5, 313-322. (Pubitemid 24310542)
-
(1994)
Human Gene Therapy
, vol.5
, Issue.3
, pp. 313-322
-
-
Lozier, J.N.1
Thompson, A.R.2
Hu, P.-C.3
Read, M.4
Brinkhous, K.M.5
High, K.A.6
Curiel, D.T.7
-
30
-
-
0001432636
-
Choice and manipulation of retroviral vectors
-
(E. J. Murray, ed.) Humana Press, Clifton, New Jersey
-
Morgenstern, J. P., and Land, H. (1991). Choice and manipulation of retroviral vectors. In "Methods in Molecular Biology: Gene Transfer and Expression Protocols" (E. J. Murray, ed.), pp. 181-206. Humana Press, Clifton, New Jersey.
-
(1991)
Methods in Molecular Biology: Gene Transfer and Expression Protocols
, pp. 181-206
-
-
Morgenstern, J.P.1
Land, H.2
-
31
-
-
0024565121
-
Production of human factor IX in animals by genetically modified skin fibroblasts: Potential therapy for hemophilia B
-
Palmer, T. D., Thompson, A. R., and Miller, A. D. (1989). Production of human factor IX in animals by genetically modified skin fibroblasts: Potential therapy for hemophilia B. Blood 73(2), 438-445. (Pubitemid 19060526)
-
(1989)
Blood
, vol.73
, Issue.2
, pp. 438-445
-
-
Palmer, T.D.1
Thompson, A.R.2
Miller, A.D.3
-
32
-
-
0028079888
-
An evaluation of receptor-mediated gene transfer using synthetic DNA-ligand complexes
-
DOI 10.1111/j.1432-1033.1994.tb20049.x
-
Perales, J. C., Ferkol, T., Molas, M., and Hanson, R. W. (1994). An evaluation of receptor-mediated gene transfer using synthetic DNA-ligand complexes. Eur. J. Biochem. 226(2), 255-266. (Pubitemid 24379043)
-
(1994)
European Journal of Biochemistry
, vol.226
, Issue.2
, pp. 255-266
-
-
Perales, J.C.1
Ferkol, T.2
Molas, M.3
Hanson, R.W.4
-
33
-
-
0023216839
-
A recombinant plasmid from which an infectious adeno-associated virus genome can be excised in vitro and its use to study viral replication
-
Samulski, R. J., Chang, L. S., and Shenk, T. E. (1987). A recombinant plasmid from which an infectious adeno-associated virus genome can be excised in vitro and its use to study viral replication. J. Virol. 61, 3096-3101. (Pubitemid 17131491)
-
(1987)
Journal of Virology
, vol.61
, Issue.10
, pp. 3096-3101
-
-
Samulski, R.J.1
Chang, L.-S.2
Shenk, T.3
-
34
-
-
0024357699
-
Absence of anti-human immunodeficiency virus types 1 and 2 seroconversion after the treatment of hemophilia A or von Willebrand's disease with pasteurized factor VIII concentrate
-
Schimpf, K., Brackman, H. H., and Kreuz, W. (1989). Absence of anti-human immunodeficiency virus types 1 and 2 seroconversion after the treatment of hemophilia A or von Willebrand's disease with pasteurized factor VIII concentrate. N. Engl. J. Med. 321, 1148-1152. (Pubitemid 19255809)
-
(1989)
New England Journal of Medicine
, vol.321
, Issue.17
, pp. 1148-1152
-
-
Schimpf, K.1
Brackmann, H.H.2
Kreuz, W.3
Kraus, B.4
Haschke, F.5
Schramm, W.6
Moesseler, J.7
Auerswald, G.8
Sutor, A.H.9
Koehler, K.10
Hellstern, P.11
Muntean, W.12
Scharrer, I.13
-
35
-
-
0023157798
-
Absence of hepatitis after treatment with a pasteurized factor VIII concentrate in patients with hemophilia and no previous transfusions
-
Schimpf, K., Mannucci, P. M., and Kreuz, W. (1987). Absence of hepatitis after treatment with a pasteurized factor VIII concentrate in patients with hemophilia and no previous transfusion. N. Engl. J. Med. 316, 918-922. (Pubitemid 17041983)
-
(1987)
New England Journal of Medicine
, vol.316
, Issue.15
, pp. 918-922
-
-
Schimpf, K.1
Mannucci, P.M.2
Kreutz, W.3
-
36
-
-
1842387143
-
An alternative approach to somatic cell gene therapy
-
St. Louis, D., and Verma, I. (1988). An alternative approach to somatic cell gene therapy. Proc. Natl. Acad. Sci. USA 85, 3150-3154.
-
(1988)
Proc. Natl. Acad. Sci. USA
, vol.85
, pp. 3150-3154
-
-
St Louis, D.1
Verma, I.2
-
37
-
-
0003024233
-
Adenovirus infection in humans
-
(H. S. Ginsberg, ed.) Plenum Press, New York
-
Strauss, S. E. (1984). Adenovirus infection in humans. In "The Adenoviruses" (H. S. Ginsberg, ed.), pp. 451-496. Plenum Press, New York.
-
(1984)
The Adenoviruses
, pp. 451-496
-
-
Strauss, S.E.1
-
38
-
-
0027387023
-
A multicenter study of viral hepatitis in a United States hemophilic population
-
Troisi, C. L., Hollinger, F. B., and Hoots, W. K. (1993). A multicenter study of viral hepatitis in a United States hemophilic population. Blood 81, 412-418. (Pubitemid 23027158)
-
(1993)
Blood
, vol.81
, Issue.2
, pp. 412-418
-
-
Troisi, C.L.1
Hollinger, F.B.2
Hoots, W.K.3
Contant, C.4
Gill, J.5
Ragni, M.6
Parmley, R.7
Sexauer, C.8
Gomperts, E.9
Buchanan, G.10
Schwartz, B.11
Adair, S.12
Fields, H.13
-
39
-
-
0025878641
-
Haemophilia A: Database of nucleotide substitutions, deletions, insertions and rearrangements of the factor VIII gene
-
Tuddenham, E. G. D., Cooper, D. N., Gitschier, J., et al., (1991). Haemophilia A: Database of nucleotide substitutions, deletions, insertions and rearrangements of the factor VIII gene. Nucleic Acids Res. 19, 4821-4833. (Pubitemid 21912862)
-
(1991)
Nucleic Acids Research
, vol.19
, Issue.18
, pp. 4821-4833
-
-
Tuddenham, E.G.D.1
Cooper, D.N.2
Gitschier, J.3
Higuchi, M.4
Hoyer, L.W.5
Yoshioka, A.6
Peake, I.R.7
Schwaab, R.8
Olek, K.9
Kazazian, H.H.10
Lavergne, J.-M.11
Giannelli, F.12
Antonarakis, S.E.13
-
40
-
-
0019958451
-
Response to infusions of polyelectrolyte fractionated human factor VIII concentrate in human haemophilia A and von Willebrand's disease
-
Tuddenham, E. G. D., Lane, R. S., Rotblat, F., Johnson, A. J., Snape, T. J., Middleton, S., Kernoff, P. B. (1982). Response to infusions of polyelectrolyte fractionated human factor VIII concentrate in human hemophilia A and von Willebrand's disease. Br. J. Hematology 52, 259-267. (Pubitemid 12033978)
-
(1982)
British Journal of Haematology
, vol.52
, Issue.2
, pp. 259-267
-
-
Tuddenham, E.G.D.1
Lane, R.S.2
Rotblat, F.3
-
41
-
-
0021677942
-
Structure of human factor VIII
-
DOI 10.1038/312337a0
-
Vehar, G., Keyt, B., Easton, D., et al., (1984). Structure of human factor VIII. Nature 313, 337-342. (Pubitemid 15209310)
-
(1984)
Nature
, vol.312
, Issue.5992
, pp. 337-342
-
-
Vehar, G.A.1
Keyt, B.2
Eaton, D.3
-
42
-
-
0029916598
-
Successful expression of human factor IX following repeat administration of an adenoviral vector in mice
-
DOI 10.1073/pnas.93.7.3056
-
Walter, J., You, Q., Hagstrom, N., Sands, M., and High, K. A. (1996). Successful expression of human factor IX following repeat administration of an adenoviral vector in mice. Proc. Natl. Acad. Sci. USA, 93, 3056-3061. (Pubitemid 26114362)
-
(1996)
Proceedings of the National Academy of Sciences of the United States of America
, vol.93
, Issue.7
, pp. 3056-3061
-
-
Walter, J.1
You, Q.2
Hagstrom, J.N.3
Sands, M.4
High, K.A.5
-
43
-
-
0028328261
-
Cellular immunity to viral antigens limits E1-deleted adenoviruses for gene therapy
-
Yang, Y., Nunes, F. A., Berencsi, K., Furth, E. E., and Gonczol, E. (1994). Cellular immunity to viral antigens limits El-deleted adenoviruses for gene therapy. Proc. Natl. Acad. Sci. USA 91, 4407-4411. (Pubitemid 24143442)
-
(1994)
Proceedings of the National Academy of Sciences of the United States of America
, vol.91
, Issue.10
, pp. 4407-4411
-
-
Yang, Y.1
Nunes, F.A.2
Berencsi, K.3
Furth, E.E.4
Gonczol, E.5
Wilson, J.M.6
-
44
-
-
0028978493
-
Recombinant IL-12 prevents formation of blocking IgA antibodies to recombinant adenovirus and allows repeated gene therapy to mouse lung
-
Yang, Y., Trinchieri, G., and Wilson, J. (1995). Recombinant IL-12 prevents formation of blocking IgA antibodies to recombinant adenovirus and allows repeated gene therapy to mouse lung. Nat. Med. 9(1), 890-893.
-
(1995)
Nat. Med.
, vol.9
, Issue.1
, pp. 890-893
-
-
Yang, Y.1
Trinchieri, G.2
Wilson, J.3
-
45
-
-
0026511128
-
Expression of human factor IX in mice after injection of genetically modified myoblasts
-
Yao, S., and Kurachi, K. (1992). Expression of human factor IX in mice after injection of genetically modified myoblasts. Proc. Natl. Acad. Sci. USA 89, 3357-3361.
-
(1992)
Proc. Natl. Acad. Sci. USA
, vol.89
, pp. 3357-3361
-
-
Yao, S.1
Kurachi, K.2
-
46
-
-
0025874746
-
Expression of human factor IX in rat capillary endothelial cells: Toward somatic gene therapy for hemophilia B
-
Yao, Y., Wilson, J. M., Nabel, E. G., Kurachi, S., and Hachiya, H. L. (1991). Expression of human factor IX in rat capillary endothelial cells: Toward somatic gene therapy for hemophilia B. Proc. Natl. Acad. Sci. USA 88, 8101-8105. (Pubitemid 21915304)
-
(1991)
Proceedings of the National Academy of Sciences of the United States of America
, vol.88
, Issue.18
, pp. 8101-8105
-
-
Yao, I.-N.1
Wilson, J.M.2
Nabeel, E.G.3
Kurachi, S.4
Hackita, H.L.5
Kurachi, K.6
-
47
-
-
0022257323
-
Nucleotide sequence of the gene for human factor IX (antihemophilic factor B)
-
DOI 10.1021/bi00335a049
-
Yoshitake, S., Schach, B. G., Foster, D. C., Davie, E. W., and Kurachi, K. (1985). Nucleotide sequence of the gene for human factor IX (antihemophilic factor B). Biochemistry 24, 3736-3750. (Pubitemid 15011912)
-
(1985)
Biochemistry
, vol.24
, Issue.14
, pp. 3736-3750
-
-
Yoshitake, S.1
Schach, B.G.2
Foster, D.C.3
-
48
-
-
0028290674
-
In vivo production of human factor VIII in mice after intrasplenic implantation of primary fibroblasts transfected by receptor-mediated, adenovirus-augmented gene delivery
-
DOI 10.1073/pnas.91.11.5148
-
Zatloukal, K., Cotten, M., Berger, M., Schmidt, W., Wagner, E., and Birnstiel, M. L. (1994). In vivo production of human factor VIII in mice after intrasplenic implantation of primary fibroblasts transfected by receptor-mediated adenovirus-augmented gene delivery. Proc. Natl. Acad. Sci. USA 91(11), 5148-5152. (Pubitemid 24177810)
-
(1994)
Proceedings of the National Academy of Sciences of the United States of America
, vol.91
, Issue.11
, pp. 5148-5152
-
-
Zatloukal, K.1
Cotten, M.2
Berger, M.3
Schmidt, W.4
Wagner, E.5
Birnstiel, M.L.6
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