메뉴 건너뛰기




Volumn 8, Issue 2, 1997, Pages 125-135

Comparison of retroviral and adeno-associated viral vectors designed to express human clotting factor IX

Author keywords

[No Author keywords available]

Indexed keywords

BLOOD CLOTTING FACTOR 9; MESSENGER RNA;

EID: 0031039171     PISSN: 10430342     EISSN: None     Source Type: Journal    
DOI: 10.1089/hum.1997.8.2-125     Document Type: Article
Times cited : (15)

References (35)
  • 1
    • 0028982236 scopus 로고
    • R-region cDNA inserts in retroviral vectors are compatible with replication and high-level protein synthesis from the insert
    • ADAM, M.A., OSBORNE, W.R.A., and MILLER, A.D. (1995). R-region cDNA inserts in retroviral vectors are compatible with replication and high-level protein synthesis from the insert. Hum. Gene Ther. 6, 1169-1176.
    • (1995) Hum. Gene Ther. , vol.6 , pp. 1169-1176
    • Adam, M.A.1    Osborne, W.R.A.2    Miller, A.D.3
  • 2
    • 0025374283 scopus 로고
    • Phenotypic correction of factor IX deficiency in skin fibroblasts of hemophilic dogs
    • AXELROD, J.H., READ, M.S., BRINKHOUS, K.M., and VERMA, I.M. (1990). Phenotypic correction of factor IX deficiency in skin fibroblasts of hemophilic dogs. Proc. Natl. Acad. Sci. USA 87, 5173-5177.
    • (1990) Proc. Natl. Acad. Sci. USA , vol.87 , pp. 5173-5177
    • Axelrod, J.H.1    Read, M.S.2    Brinkhous, K.M.3    Verma, I.M.4
  • 3
    • 0025316898 scopus 로고
    • Development of a high-liter retrovirus producer cell line capable of gene transfer into rhesus monkey hematopoietic stem cells
    • BODINE, D.M., MCDONAGH, K.T., BRANDT, S.J., NEY, P.A., AGRICOLA, B., BYRNE, E., and NIENHUIS, A.W. (1990). Development of a high-liter retrovirus producer cell line capable of gene transfer into rhesus monkey hematopoietic stem cells. Proc. Natl. Acad. Sci. USA 87, 3738-3742.
    • (1990) Proc. Natl. Acad. Sci. USA , vol.87 , pp. 3738-3742
    • Bodine, D.M.1    Mcdonagh, K.T.2    Brandt, S.J.3    Ney, P.A.4    Agricola, B.5    Byrne, E.6    Nienhuis, A.W.7
  • 4
    • 0028230779 scopus 로고
    • Lack of expression from a retroviral vector after transduction of murine hematopoietic stem cells is associated with methylation in vivo
    • CHALLITA, P.M., and KOHN, D.B. (1994). Lack of expression from a retroviral vector after transduction of murine hematopoietic stem cells is associated with methylation in vivo. Proc. Natl. Acad. Sci. USA 91, 2567-2571.
    • (1994) Proc. Natl. Acad. Sci. USA , vol.91 , pp. 2567-2571
    • Challita, P.M.1    Kohn, D.B.2
  • 5
    • 0028815676 scopus 로고
    • Multiple modifications in cis elements of the long terminal repeat of retroviral vectors lead to increased expression and decreased DNA methylation in embryonic carcinoma cells
    • CHALLITA, P., SKELTON, D., EL-KHOUEIRY, A., YU, X., WEINBERG, K., AND KOHN, D.B. (1985). Multiple modifications in cis elements of the long terminal repeat of retroviral vectors lead to increased expression and decreased DNA methylation in embryonic carcinoma cells. J. Virol. 69, 748-755.
    • (1985) J. Virol. , vol.69 , pp. 748-755
    • Challita, P.1    Skelton, D.2    El-Khoueiry, A.3    Yu, X.4    Weinberg, K.5    Kohn, D.B.6
  • 6
    • 0029618739 scopus 로고
    • High-efficiency transfer of the T cell co-stimulatory molecule B7-2 to lymphoid cells using high-titer recombinant adeno-associated virus vectors
    • CHIORINI, J.A, WENDTNER, C.M., URCELAY, E., SAFER, B., HALLEK, M., and KOTIN, R.M. (1995). High-efficiency transfer of the T cell co-stimulatory molecule B7-2 to lymphoid cells using high-titer recombinant adeno-associated virus vectors. Hum. Gene Ther. 6, 1531-1541.
    • (1995) Hum. Gene Ther. , vol.6 , pp. 1531-1541
    • Chiorini, J.A.1    Wendtner, C.M.2    Urcelay, E.3    Safer, B.4    Hallek, M.5    Kotin, R.M.6
  • 7
    • 0028805939 scopus 로고
    • Development and analysis of retroviral vectors expressing human factor VIII as a potential gene therapy for hemophilia A
    • CHUAH, M.K.L., VANDENDRIESSCHE, T., and MORGAN, R.A. (1995). Development and analysis of retroviral vectors expressing human factor VIII as a potential gene therapy for hemophilia A. Hum. Gene Ther. 6, 1363-1377.
    • (1995) Hum. Gene Ther. , vol.6 , pp. 1363-1377
    • Chuah, M.K.L.1    Vandendriessche, T.2    Morgan, R.A.3
  • 8
    • 0028170357 scopus 로고
    • Retroviral vectors containing chimeric promoter/enhancer elements exhibit cell-type-specific gene expression
    • COUTURE, L.A., MULLEN C.A., and MORGAN, R.A. (1994). Retroviral vectors containing chimeric promoter/enhancer elements exhibit cell-type-specific gene expression. Hum. Gene Ther. 5, 667-677.
    • (1994) Hum. Gene Ther. , vol.5 , pp. 667-677
    • Couture, L.A.1    Mullen, C.A.2    Morgan, R.A.3
  • 9
    • 0025286228 scopus 로고
    • Disruption of a C/EBP binding site in the factor IX promoter is associated with haemophilia B
    • CROSSLEY, M., and BROWNLEE, G.G. (1990). Disruption of a C/EBP binding site in the factor IX promoter is associated with haemophilia B. Science 345, 444-446.
    • (1990) Science , vol.345 , pp. 444-446
    • Crossley, M.1    Brownlee, G.G.2
  • 10
    • 0026486612 scopus 로고
    • Gene therapy via primary myoblasts: Long term expression of factor IX protein following transplantation in vivo
    • DAI, Y., ROMAN, M., NAVIAUX, R.K., and VERMA, I.M. (1992). Gene therapy via primary myoblasts: Long term expression of factor IX protein following transplantation in vivo. Proc. Natl. Acad. Sci. USA 89, 10892-10895.
    • (1992) Proc. Natl. Acad. Sci. USA , vol.89 , pp. 10892-10895
    • Dai, Y.1    Roman, M.2    Naviaux, R.K.3    Verma, I.M.4
  • 11
    • 0026625009 scopus 로고
    • Recombinant retroviruses as tools for gene transfer to somatic cells
    • DANOS, O., and HEARD, J.M. (1992). Recombinant retroviruses as tools for gene transfer to somatic cells. Bone Marrow Transplant. 9, 131-138.
    • (1992) Bone Marrow Transplant. , vol.9 , pp. 131-138
    • Danos, O.1    Heard, J.M.2
  • 15
    • 0029151404 scopus 로고
    • Adeno-associated virus vectors for gene therapy
    • FLOTTE, T.R., and CARTER, B.J. (1995). Adeno-associated virus vectors for gene therapy. Gene Ther. 2, 357-362.
    • (1995) Gene Ther. , vol.2 , pp. 357-362
    • Flotte, T.R.1    Carter, B.J.2
  • 16
    • 0027465539 scopus 로고
    • Towards gene therapy for haemophilia B using primary human keratinocytes
    • GERRARD, A.J., HUDSON, D.L., BROWNLEE, G.G., and WATT, F.M. (1993). Towards gene therapy for haemophilia B using primary human keratinocytes. Nature Genet. 3, 180-184.
    • (1993) Nature Genet. , vol.3 , pp. 180-184
    • Gerrard, A.J.1    Hudson, D.L.2    Brownlee, G.G.3    Watt, F.M.4
  • 18
    • 0028170362 scopus 로고
    • Prospects for the use of adeno-associated virus as a vector for human gene therapy
    • KOTIN, R.M. (1994). Prospects for the use of adeno-associated virus as a vector for human gene therapy. Hum. Gene Ther. 5, 793-801.
    • (1994) Hum. Gene Ther. , vol.5 , pp. 793-801
    • Kotin, R.M.1
  • 20
    • 0020788648 scopus 로고
    • Cloning of infectious adeno-associated virus genomes in bacterial plasmids
    • LAUGHLIN, C.A., TRATSCHIN, J., COON, H., and CARTER, B.J. (1983). Cloning of infectious adeno-associated virus genomes in bacterial plasmids. Gene 23, 65-73.
    • (1983) Gene , vol.23 , pp. 65-73
    • Laughlin, C.A.1    Tratschin, J.2    Coon, H.3    Carter, B.J.4
  • 21
  • 22
    • 0023871422 scopus 로고
    • A safe packaging cell line for gene transfer: Separating viral genes on two different plasmids
    • MARKOWITZ, D., GOFF, S., and BANK, A. (1988). A safe packaging cell line for gene transfer: Separating viral genes on two different plasmids. J. Virol. 62, 1120-1124.
    • (1988) J. Virol. , vol.62 , pp. 1120-1124
    • Markowitz, D.1    Goff, S.2    Bank, A.3
  • 23
  • 24
    • 0022767368 scopus 로고
    • Redesign of retroviral packaging cell lines to avoid recombination leading to helper virus reproduction
    • MILLER, A.D., and BUTTIMORE, C. (1986). Redesign of retroviral packaging cell lines to avoid recombination leading to helper virus reproduction. Mol. Cell. Biol. 6, 2895-2903.
    • (1986) Mol. Cell. Biol. , vol.6 , pp. 2895-2903
    • Miller, A.D.1    Buttimore, C.2
  • 25
    • 0026588638 scopus 로고
    • Retroviral vectors containing putative internal ribosome entry sites: Development of apolycistronic gene transfer system and application of human gene therapy
    • MORGAN, R.A., COUTURE, L., ELROY-STEIN, O., RAGHEB, J., MOSS, B., and ANDERSON, W.F. (1992). Retroviral vectors containing putative internal ribosome entry sites: development of apolycistronic gene transfer system and application of human gene therapy. Nucleic Acids Res. 20, 1293-1299.
    • (1992) Nucleic Acids Res. , vol.20 , pp. 1293-1299
    • Morgan, R.A.1    Couture, L.2    Elroy-Stein, O.3    Ragheb, J.4    Moss, B.5    Anderson, W.F.6
  • 26
    • 0024565121 scopus 로고
    • Production of human factor IX in animal by genetically modified fibroblasts: Potential therapy for hemophilia B
    • PALMER, T.D., THOMPSON, A.R., and MILLER, A.D. (1989). Production of human factor IX in animal by genetically modified fibroblasts: Potential therapy for hemophilia B. Blood 72, 438-445.
    • (1989) Blood , vol.72 , pp. 438-445
    • Palmer, T.D.1    Thompson, A.R.2    Miller, A.D.3
  • 27
    • 0025976935 scopus 로고
    • Genetically modified skin fibroblasts persist long after transplantation but gradually inactivate introduced genes
    • PALMER, T.D., ROSMAN, G.J., OSBORNE, W.R.A., and MILLER, A.D. (1991). Genetically modified skin fibroblasts persist long after transplantation but gradually inactivate introduced genes. Proc. Natl. Acad. Sci. USA 88, 1330-1334.
    • (1991) Proc. Natl. Acad. Sci. USA , vol.88 , pp. 1330-1334
    • Palmer, T.D.1    Rosman, G.J.2    Osborne, W.R.A.3    Miller, A.D.4
  • 29
    • 0025753128 scopus 로고
    • Long-term in vivo expression of retrovirus-mediated gene transfer in mouse fibroblast implants
    • SCHARFMANN, R., AXELROD, J.H., and VERMA, I.M. (1991). Long-term in vivo expression of retrovirus-mediated gene transfer in mouse fibroblast implants. Proc. Natl. Acad. Sci. USA 88, 4626-4630.
    • (1991) Proc. Natl. Acad. Sci. USA , vol.88 , pp. 4626-4630
    • Scharfmann, R.1    Axelrod, J.H.2    Verma, I.M.3
  • 31
    • 0029916598 scopus 로고    scopus 로고
    • Successful expression of human factor IX following repeat administration of an adenoviral vector in mice
    • WALTER, J., YOU, Q., HAGSTROM, J.N., SANDS, M., and HIGH, K.A. (1996). Successful expression of human factor IX following repeat administration of an adenoviral vector in mice. Proc. Natl. Acad. Sci. USA 93, 3056-3061.
    • (1996) Proc. Natl. Acad. Sci. USA , vol.93 , pp. 3056-3061
    • Walter, J.1    You, Q.2    Hagstrom, J.N.3    Sands, M.4    High, K.A.5
  • 32
    • 0026511128 scopus 로고
    • Expression of human factor IX in mice after injection of genetically modified myoblasts
    • YAO, S., and KURACHI, K. (1992). Expression of human factor IX in mice after injection of genetically modified myoblasts. Proc. Natl. Acad. Sci. USA 89, 3357-3361.
    • (1992) Proc. Natl. Acad. Sci. USA , vol.89 , pp. 3357-3361
    • Yao, S.1    Kurachi, K.2
  • 33
    • 0025874746 scopus 로고
    • Expression of human factor IX in rat capillary endothelial cells: Toward somatic gene therapy for human hemophilia B
    • YAO, S., WILSOM, J.M., NABEL, E.G., KURACHI, S., HACHIYA, H.L., and KURACHI, K. (1991). Expression of human factor IX in rat capillary endothelial cells: toward somatic gene therapy for human hemophilia B. Proc. Natl. Acad. Sci. USA 88, 8101-8105.
    • (1991) Proc. Natl. Acad. Sci. USA , vol.88 , pp. 8101-8105
    • Yao, S.1    Wilsom, J.M.2    Nabel, E.G.3    Kurachi, S.4    Hachiya, H.L.5    Kurachi, K.6
  • 34
    • 0028386527 scopus 로고
    • Primary myoblast-mediated gene transfer: Persistent expression of human factor IX in mice
    • YAO, S., SMITH, K.J., and KURACHI, K. (1994). Primary myoblast-mediated gene transfer: persistent expression of human factor IX in mice. Gene Ther. 1, 99-107.
    • (1994) Gene Ther. , vol.1 , pp. 99-107
    • Yao, S.1    Smith, K.J.2    Kurachi, K.3
  • 35
    • 16944363881 scopus 로고
    • Long term expression of human of human factor IX cDNA in rabbits
    • ZHOU, J., QIU, X., LU, D., LU, J., and HSUEN, J.L. (1993). Long term expression of human of human factor IX cDNA in rabbits. Science in China (series B) 36, 33-41.
    • (1993) Science in China (Series B) , vol.36 , pp. 33-41
    • Zhou, J.1    Qiu, X.2    Lu, D.3    Lu, J.4    Hsuen, J.L.5


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.