-
1
-
-
0028982236
-
R-region cDNA inserts in retroviral vectors are compatible with replication and high-level protein synthesis from the insert
-
ADAM, M.A., OSBORNE, W.R.A., and MILLER, A.D. (1995). R-region cDNA inserts in retroviral vectors are compatible with replication and high-level protein synthesis from the insert. Hum. Gene Ther. 6, 1169-1176.
-
(1995)
Hum. Gene Ther.
, vol.6
, pp. 1169-1176
-
-
Adam, M.A.1
Osborne, W.R.A.2
Miller, A.D.3
-
2
-
-
0025374283
-
Phenotypic correction of factor IX deficiency in skin fibroblasts of hemophilic dogs
-
AXELROD, J.H., READ, M.S., BRINKHOUS, K.M., and VERMA, I.M. (1990). Phenotypic correction of factor IX deficiency in skin fibroblasts of hemophilic dogs. Proc. Natl. Acad. Sci. USA 87, 5173-5177.
-
(1990)
Proc. Natl. Acad. Sci. USA
, vol.87
, pp. 5173-5177
-
-
Axelrod, J.H.1
Read, M.S.2
Brinkhous, K.M.3
Verma, I.M.4
-
3
-
-
0025316898
-
Development of a high-liter retrovirus producer cell line capable of gene transfer into rhesus monkey hematopoietic stem cells
-
BODINE, D.M., MCDONAGH, K.T., BRANDT, S.J., NEY, P.A., AGRICOLA, B., BYRNE, E., and NIENHUIS, A.W. (1990). Development of a high-liter retrovirus producer cell line capable of gene transfer into rhesus monkey hematopoietic stem cells. Proc. Natl. Acad. Sci. USA 87, 3738-3742.
-
(1990)
Proc. Natl. Acad. Sci. USA
, vol.87
, pp. 3738-3742
-
-
Bodine, D.M.1
Mcdonagh, K.T.2
Brandt, S.J.3
Ney, P.A.4
Agricola, B.5
Byrne, E.6
Nienhuis, A.W.7
-
4
-
-
0028230779
-
Lack of expression from a retroviral vector after transduction of murine hematopoietic stem cells is associated with methylation in vivo
-
CHALLITA, P.M., and KOHN, D.B. (1994). Lack of expression from a retroviral vector after transduction of murine hematopoietic stem cells is associated with methylation in vivo. Proc. Natl. Acad. Sci. USA 91, 2567-2571.
-
(1994)
Proc. Natl. Acad. Sci. USA
, vol.91
, pp. 2567-2571
-
-
Challita, P.M.1
Kohn, D.B.2
-
5
-
-
0028815676
-
Multiple modifications in cis elements of the long terminal repeat of retroviral vectors lead to increased expression and decreased DNA methylation in embryonic carcinoma cells
-
CHALLITA, P., SKELTON, D., EL-KHOUEIRY, A., YU, X., WEINBERG, K., AND KOHN, D.B. (1985). Multiple modifications in cis elements of the long terminal repeat of retroviral vectors lead to increased expression and decreased DNA methylation in embryonic carcinoma cells. J. Virol. 69, 748-755.
-
(1985)
J. Virol.
, vol.69
, pp. 748-755
-
-
Challita, P.1
Skelton, D.2
El-Khoueiry, A.3
Yu, X.4
Weinberg, K.5
Kohn, D.B.6
-
6
-
-
0029618739
-
High-efficiency transfer of the T cell co-stimulatory molecule B7-2 to lymphoid cells using high-titer recombinant adeno-associated virus vectors
-
CHIORINI, J.A, WENDTNER, C.M., URCELAY, E., SAFER, B., HALLEK, M., and KOTIN, R.M. (1995). High-efficiency transfer of the T cell co-stimulatory molecule B7-2 to lymphoid cells using high-titer recombinant adeno-associated virus vectors. Hum. Gene Ther. 6, 1531-1541.
-
(1995)
Hum. Gene Ther.
, vol.6
, pp. 1531-1541
-
-
Chiorini, J.A.1
Wendtner, C.M.2
Urcelay, E.3
Safer, B.4
Hallek, M.5
Kotin, R.M.6
-
7
-
-
0028805939
-
Development and analysis of retroviral vectors expressing human factor VIII as a potential gene therapy for hemophilia A
-
CHUAH, M.K.L., VANDENDRIESSCHE, T., and MORGAN, R.A. (1995). Development and analysis of retroviral vectors expressing human factor VIII as a potential gene therapy for hemophilia A. Hum. Gene Ther. 6, 1363-1377.
-
(1995)
Hum. Gene Ther.
, vol.6
, pp. 1363-1377
-
-
Chuah, M.K.L.1
Vandendriessche, T.2
Morgan, R.A.3
-
8
-
-
0028170357
-
Retroviral vectors containing chimeric promoter/enhancer elements exhibit cell-type-specific gene expression
-
COUTURE, L.A., MULLEN C.A., and MORGAN, R.A. (1994). Retroviral vectors containing chimeric promoter/enhancer elements exhibit cell-type-specific gene expression. Hum. Gene Ther. 5, 667-677.
-
(1994)
Hum. Gene Ther.
, vol.5
, pp. 667-677
-
-
Couture, L.A.1
Mullen, C.A.2
Morgan, R.A.3
-
9
-
-
0025286228
-
Disruption of a C/EBP binding site in the factor IX promoter is associated with haemophilia B
-
CROSSLEY, M., and BROWNLEE, G.G. (1990). Disruption of a C/EBP binding site in the factor IX promoter is associated with haemophilia B. Science 345, 444-446.
-
(1990)
Science
, vol.345
, pp. 444-446
-
-
Crossley, M.1
Brownlee, G.G.2
-
10
-
-
0026486612
-
Gene therapy via primary myoblasts: Long term expression of factor IX protein following transplantation in vivo
-
DAI, Y., ROMAN, M., NAVIAUX, R.K., and VERMA, I.M. (1992). Gene therapy via primary myoblasts: Long term expression of factor IX protein following transplantation in vivo. Proc. Natl. Acad. Sci. USA 89, 10892-10895.
-
(1992)
Proc. Natl. Acad. Sci. USA
, vol.89
, pp. 10892-10895
-
-
Dai, Y.1
Roman, M.2
Naviaux, R.K.3
Verma, I.M.4
-
11
-
-
0026625009
-
Recombinant retroviruses as tools for gene transfer to somatic cells
-
DANOS, O., and HEARD, J.M. (1992). Recombinant retroviruses as tools for gene transfer to somatic cells. Bone Marrow Transplant. 9, 131-138.
-
(1992)
Bone Marrow Transplant.
, vol.9
, pp. 131-138
-
-
Danos, O.1
Heard, J.M.2
-
13
-
-
0026321996
-
Retroviral vector mediated in vivo expression of low density lipoprotein receptors in the watanabe heritable hyperlipidemic rabbit
-
DICHEK, D.A., BRATTHAUER, G.L., BEG, Z.H., ANDERSON, K.D., NEWMAN, K.D., ZWIEBEL, J.A., HOEG, J.M., and ANDERSON, W.F. (1991). Retroviral vector mediated in vivo expression of low density lipoprotein receptors in the watanabe heritable hyperlipidemic rabbit. Somat. Cell Mol. Genet. 17, 287-301.
-
(1991)
Somat. Cell Mol. Genet.
, vol.17
, pp. 287-301
-
-
Dichek, D.A.1
Bratthauer, G.L.2
Beg, Z.H.3
Anderson, K.D.4
Newman, K.D.5
Zwiebel, J.A.6
Hoeg, J.M.7
Anderson, W.F.8
-
14
-
-
0029154012
-
Gene therapy for hemophilia B: Host immunosuppression prolongs the therapeutic effect of adenovirus-mediated factor IX expression
-
FANG, B., EISENSMITH, R.C., WANG, H., KAY, M.A., CROSS, R.E., LANDEN, C.N., GORDON, G., BELLINGER, D.A., READ, M.S., HU, P.C., BRINKHOUS, K.M., and WOO, S.L.C. (1995). Gene therapy for hemophilia B: Host immunosuppression prolongs the therapeutic effect of adenovirus-mediated factor IX expression. Hum. Gene Ther. 6, 1039-1044.
-
(1995)
Hum. Gene Ther.
, vol.6
, pp. 1039-1044
-
-
Fang, B.1
Eisensmith, R.C.2
Wang, H.3
Kay, M.A.4
Cross, R.E.5
Landen, C.N.6
Gordon, G.7
Bellinger, D.A.8
Read, M.S.9
Hu, P.C.10
Brinkhous, K.M.11
Woo, S.L.C.12
-
15
-
-
0029151404
-
Adeno-associated virus vectors for gene therapy
-
FLOTTE, T.R., and CARTER, B.J. (1995). Adeno-associated virus vectors for gene therapy. Gene Ther. 2, 357-362.
-
(1995)
Gene Ther.
, vol.2
, pp. 357-362
-
-
Flotte, T.R.1
Carter, B.J.2
-
16
-
-
0027465539
-
Towards gene therapy for haemophilia B using primary human keratinocytes
-
GERRARD, A.J., HUDSON, D.L., BROWNLEE, G.G., and WATT, F.M. (1993). Towards gene therapy for haemophilia B using primary human keratinocytes. Nature Genet. 3, 180-184.
-
(1993)
Nature Genet.
, vol.3
, pp. 180-184
-
-
Gerrard, A.J.1
Hudson, D.L.2
Brownlee, G.G.3
Watt, F.M.4
-
17
-
-
0027686238
-
In vivo gene therapy of hemophilia B: Sustained partial correction in factor IX deficient dogs
-
KAY, M.A., ROTHENBERG, S., LANDEN, C.N., BELLINGER, D.A., LELAND, F., TOMAN, C., FINEGOLD, M., THOMPSON, A.R., READ, M.S., BRINKHOUS, K.M., and WOO, S.L.C. (1993). In vivo gene therapy of hemophilia B: sustained partial correction in factor IX deficient dogs. Science 262, 117-119.
-
(1993)
Science
, vol.262
, pp. 117-119
-
-
Kay, M.A.1
Rothenberg, S.2
Landen, C.N.3
Bellinger, D.A.4
Leland, F.5
Toman, C.6
Finegold, M.7
Thompson, A.R.8
Read, M.S.9
Brinkhous, K.M.10
Woo, S.L.C.11
-
18
-
-
0028170362
-
Prospects for the use of adeno-associated virus as a vector for human gene therapy
-
KOTIN, R.M. (1994). Prospects for the use of adeno-associated virus as a vector for human gene therapy. Hum. Gene Ther. 5, 793-801.
-
(1994)
Hum. Gene Ther.
, vol.5
, pp. 793-801
-
-
Kotin, R.M.1
-
19
-
-
0027732257
-
Biology of Factor IX
-
KURACHI, K., KURACHI, S., and YAO, S. (1993). Biology of Factor IX. Blood Coagul. Fibrinol. 4, 953-974.
-
(1993)
Blood Coagul. Fibrinol.
, vol.4
, pp. 953-974
-
-
Kurachi, K.1
Kurachi, S.2
Yao, S.3
-
20
-
-
0020788648
-
Cloning of infectious adeno-associated virus genomes in bacterial plasmids
-
LAUGHLIN, C.A., TRATSCHIN, J., COON, H., and CARTER, B.J. (1983). Cloning of infectious adeno-associated virus genomes in bacterial plasmids. Gene 23, 65-73.
-
(1983)
Gene
, vol.23
, pp. 65-73
-
-
Laughlin, C.A.1
Tratschin, J.2
Coon, H.3
Carter, B.J.4
-
22
-
-
0023871422
-
A safe packaging cell line for gene transfer: Separating viral genes on two different plasmids
-
MARKOWITZ, D., GOFF, S., and BANK, A. (1988). A safe packaging cell line for gene transfer: Separating viral genes on two different plasmids. J. Virol. 62, 1120-1124.
-
(1988)
J. Virol.
, vol.62
, pp. 1120-1124
-
-
Markowitz, D.1
Goff, S.2
Bank, A.3
-
23
-
-
0027228057
-
Factors affecting retroviral vector function and structural integrity
-
MCLACHLIN, J.R., MITTEREDER, N., DAUCHER, M.B., KADAN, M., and EGLITIS, M.A. (1993). Factors affecting retroviral vector function and structural integrity. Virology 195, 1-5.
-
(1993)
Virology
, vol.195
, pp. 1-5
-
-
Mclachlin, J.R.1
Mittereder, N.2
Daucher, M.B.3
Kadan, M.4
Eglitis, M.A.5
-
24
-
-
0022767368
-
Redesign of retroviral packaging cell lines to avoid recombination leading to helper virus reproduction
-
MILLER, A.D., and BUTTIMORE, C. (1986). Redesign of retroviral packaging cell lines to avoid recombination leading to helper virus reproduction. Mol. Cell. Biol. 6, 2895-2903.
-
(1986)
Mol. Cell. Biol.
, vol.6
, pp. 2895-2903
-
-
Miller, A.D.1
Buttimore, C.2
-
25
-
-
0026588638
-
Retroviral vectors containing putative internal ribosome entry sites: Development of apolycistronic gene transfer system and application of human gene therapy
-
MORGAN, R.A., COUTURE, L., ELROY-STEIN, O., RAGHEB, J., MOSS, B., and ANDERSON, W.F. (1992). Retroviral vectors containing putative internal ribosome entry sites: development of apolycistronic gene transfer system and application of human gene therapy. Nucleic Acids Res. 20, 1293-1299.
-
(1992)
Nucleic Acids Res.
, vol.20
, pp. 1293-1299
-
-
Morgan, R.A.1
Couture, L.2
Elroy-Stein, O.3
Ragheb, J.4
Moss, B.5
Anderson, W.F.6
-
26
-
-
0024565121
-
Production of human factor IX in animal by genetically modified fibroblasts: Potential therapy for hemophilia B
-
PALMER, T.D., THOMPSON, A.R., and MILLER, A.D. (1989). Production of human factor IX in animal by genetically modified fibroblasts: Potential therapy for hemophilia B. Blood 72, 438-445.
-
(1989)
Blood
, vol.72
, pp. 438-445
-
-
Palmer, T.D.1
Thompson, A.R.2
Miller, A.D.3
-
27
-
-
0025976935
-
Genetically modified skin fibroblasts persist long after transplantation but gradually inactivate introduced genes
-
PALMER, T.D., ROSMAN, G.J., OSBORNE, W.R.A., and MILLER, A.D. (1991). Genetically modified skin fibroblasts persist long after transplantation but gradually inactivate introduced genes. Proc. Natl. Acad. Sci. USA 88, 1330-1334.
-
(1991)
Proc. Natl. Acad. Sci. USA
, vol.88
, pp. 1330-1334
-
-
Palmer, T.D.1
Rosman, G.J.2
Osborne, W.R.A.3
Miller, A.D.4
-
28
-
-
0003903343
-
-
Cold Spring Harbor Laboratory Press, Cold Spring Harbor, NY
-
SAMBROOK, J., FRITSCH, E.F., and MANIATIS, T. (1989). Molecular Cloning: A Laboratory Manual. (Cold Spring Harbor Laboratory Press, Cold Spring Harbor, NY) pp. 9.31-9.58, 7.37-7.79.
-
(1989)
Molecular Cloning: A Laboratory Manual
-
-
Sambrook, J.1
Fritsch, E.F.2
Maniatis, T.3
-
29
-
-
0025753128
-
Long-term in vivo expression of retrovirus-mediated gene transfer in mouse fibroblast implants
-
SCHARFMANN, R., AXELROD, J.H., and VERMA, I.M. (1991). Long-term in vivo expression of retrovirus-mediated gene transfer in mouse fibroblast implants. Proc. Natl. Acad. Sci. USA 88, 4626-4630.
-
(1991)
Proc. Natl. Acad. Sci. USA
, vol.88
, pp. 4626-4630
-
-
Scharfmann, R.1
Axelrod, J.H.2
Verma, I.M.3
-
30
-
-
0027521773
-
Adenovirus mediated expression of therapeutic plasma levels of human factor IX in mice
-
SMITH, T.A., MEHAFFEY, M.G., KAYDA, D.B., SAUNDERS, J.M., YEI, S., TRAPNELL, B.C., MCCLELLAND, A., and KALEKO, M. (1993). Adenovirus mediated expression of therapeutic plasma levels of human factor IX in mice. Nature Genet. 5, 397-402.
-
(1993)
Nature Genet.
, vol.5
, pp. 397-402
-
-
Smith, T.A.1
Mehaffey, M.G.2
Kayda, D.B.3
Saunders, J.M.4
Yei, S.5
Trapnell, B.C.6
Mcclelland, A.7
Kaleko, M.8
-
31
-
-
0029916598
-
Successful expression of human factor IX following repeat administration of an adenoviral vector in mice
-
WALTER, J., YOU, Q., HAGSTROM, J.N., SANDS, M., and HIGH, K.A. (1996). Successful expression of human factor IX following repeat administration of an adenoviral vector in mice. Proc. Natl. Acad. Sci. USA 93, 3056-3061.
-
(1996)
Proc. Natl. Acad. Sci. USA
, vol.93
, pp. 3056-3061
-
-
Walter, J.1
You, Q.2
Hagstrom, J.N.3
Sands, M.4
High, K.A.5
-
32
-
-
0026511128
-
Expression of human factor IX in mice after injection of genetically modified myoblasts
-
YAO, S., and KURACHI, K. (1992). Expression of human factor IX in mice after injection of genetically modified myoblasts. Proc. Natl. Acad. Sci. USA 89, 3357-3361.
-
(1992)
Proc. Natl. Acad. Sci. USA
, vol.89
, pp. 3357-3361
-
-
Yao, S.1
Kurachi, K.2
-
33
-
-
0025874746
-
Expression of human factor IX in rat capillary endothelial cells: Toward somatic gene therapy for human hemophilia B
-
YAO, S., WILSOM, J.M., NABEL, E.G., KURACHI, S., HACHIYA, H.L., and KURACHI, K. (1991). Expression of human factor IX in rat capillary endothelial cells: toward somatic gene therapy for human hemophilia B. Proc. Natl. Acad. Sci. USA 88, 8101-8105.
-
(1991)
Proc. Natl. Acad. Sci. USA
, vol.88
, pp. 8101-8105
-
-
Yao, S.1
Wilsom, J.M.2
Nabel, E.G.3
Kurachi, S.4
Hachiya, H.L.5
Kurachi, K.6
-
34
-
-
0028386527
-
Primary myoblast-mediated gene transfer: Persistent expression of human factor IX in mice
-
YAO, S., SMITH, K.J., and KURACHI, K. (1994). Primary myoblast-mediated gene transfer: persistent expression of human factor IX in mice. Gene Ther. 1, 99-107.
-
(1994)
Gene Ther.
, vol.1
, pp. 99-107
-
-
Yao, S.1
Smith, K.J.2
Kurachi, K.3
-
35
-
-
16944363881
-
Long term expression of human of human factor IX cDNA in rabbits
-
ZHOU, J., QIU, X., LU, D., LU, J., and HSUEN, J.L. (1993). Long term expression of human of human factor IX cDNA in rabbits. Science in China (series B) 36, 33-41.
-
(1993)
Science in China (Series B)
, vol.36
, pp. 33-41
-
-
Zhou, J.1
Qiu, X.2
Lu, D.3
Lu, J.4
Hsuen, J.L.5
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