High-level globin gene expression mediated by a recombinant adeno- associated virus genome that contains the 3' γ globin gene regulatory element and integrates as tandem copies in erythroid cells

Blood

Volumn 89, Issue 6, 1997, Pages 2167-2175

  Hargrove, Phillip W ^b   Vanin, Elio F ^b   Kurtzman, Gary J ^b   Nienhuis, Arthur W ^a  

^a ST JUDE CHILDREN S RESEARCH HOSPITAL   (United States)

^b NONE

Author keywords

[No Author keywords available]

Indexed keywords

GAMMA GLOBIN; GLOBIN; MESSENGER RNA;

ADENOVIRUS; ARTICLE; CELL IMMORTALIZATION; CELL STRAIN K 562; ERYTHROID CELL; GENE EXPRESSION REGULATION; GENE LOCUS; GENE MUTATION; GENE THERAPY; GENE TRANSFER; HUMAN; HUMAN CELL; PRIORITY JOURNAL; REGULATOR GENE; VIRUS GENOME; VIRUS RECOMBINANT;

EID: 0030999174     PISSN: 00064971     EISSN: None     Source Type: Journal    
DOI: 10.1182/blood.v89.6.2167     Document Type: Article

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