Keratinocyte gene therapy for adenosine deaminase deficiency: A model approach for inherited metabolic disorders

Human Gene Therapy

Volumn 8, Issue 8, 1997, Pages 911-917

  Fenjves, Elizabeth S ^a   Schwartz, Pauline M ^b   Blaese, R Michael ^c   Taichman, Lorne B ^a  

^a STONY BROOK UNIVERSITY   (United States)

^b YALE UNIVERSITY SCHOOL OF MEDICINE   (United States)

^c NATIONAL HUMAN GENOME RESEARCH INSTITUTE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ADENOSINE DEAMINASE; DEOXYADENOSINE; MESSENGER RNA; VIRUS VECTOR;

ARTICLE; CASE REPORT; CELL CULTURE; CONTROLLED STUDY; DEAMINATION; ENZYME ACTIVITY; ENZYME DEFICIENCY; ENZYME REPLACEMENT; ENZYME SUBSTRATE; EPIDERMIS; EXTRACELLULAR FLUID; GENE THERAPY; GENETIC TRANSDUCTION; HUMAN; HUMAN CELL; IN VITRO STUDY; KERATINOCYTE; METABOLIC DISORDER; MICHAELIS MENTEN KINETICS; RETROVIRUS;

EID: 0030918639     PISSN: 10430342     EISSN: None     Source Type: Journal    
DOI: 10.1089/hum.1997.8.8-911     Document Type: Article

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