Restoration of β-globin gene expression in mammalian cells by antisense oligonucleotides that modify the aberrant splicing patterns of thalassemic pre-mRNAs

Nucleosides and Nucleotides

Volumn 16, Issue 7-9, 1997, Pages 1173-1182

  Sierakowska, Halina ^b   Montague, Michael ^a   Agrawal, Sudhir ^c   Kole, Ryszard ^a  

^a UNIVERSITY OF NORTH CAROLINA SCHOOL OF MEDICINE   (United States)

^b INSTITUTE OF BIOCHEMISTRY AND BIOPHYSICS   (Poland)

^c HYBRIDON INC   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ANTISENSE OLIGONUCLEOTIDE; BETA GLOBIN; CELLFECTIN; DMRIE C; DRUG CARRIER; LIPOFECTAMINE; LIPOSOME; MESSENGER RNA PRECURSOR; UNCLASSIFIED DRUG;

ANIMAL CELL; CONFERENCE PAPER; DRUG FORMULATION; GENE ACTIVATION; GENE EXPRESSION; GENE THERAPY; HUMAN; HUMAN CELL; NONHUMAN; PROTEIN ANALYSIS; RNA ANALYSIS; RNA SPLICING; THALASSEMIA;

ANIMALIA; MAMMALIA;

EID: 0030832989     PISSN: 07328311     EISSN: None     Source Type: Journal    
DOI: 10.1080/07328319708006154     Document Type: Conference Paper

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