Evaluation of β-globin gene therapy constructs in single copy transgenic mice

Nucleic Acids Research

Volumn 25, Issue 6, 1997, Pages 1296-1302

  Ellis, James ^b   Pasceri, Peter ^f   Tan Un, Kian C ^a,c   Wu, Xiumei ^f   Harper, Alex ^a,d   Fraser, Peter ^a,e   Grosveld, Frank ^a,e  

^a NATIONAL INSTITUTE FOR MEDICAL RESEARCH   (United Kingdom)

^b HOSPITAL FOR SICK CHILDREN   (Canada)

^c UNIVERSITY OF HONG KONG   (Hong Kong)

^d ST THOMAS HOSPITAL   (United Kingdom)

^e ERASMUS MEDICAL CENTER   (Netherlands)

^f NONE

Author keywords

[No Author keywords available]

Indexed keywords

BETA GLOBIN;

ADENO ASSOCIATED VIRUS; ANIMAL EXPERIMENT; ANIMAL TISSUE; ARTICLE; BETA THALASSEMIA; FETUS; GENE LOCUS; GENE NUMBER; GENE THERAPY; GENETIC TRANSDUCTION; MOUSE; NONHUMAN; PRIORITY JOURNAL; PROMOTER REGION; RETROVIRUS; TRANSGENE;

ANIMALS; DIMERIZATION; DNA PRIMERS; DNA TRANSPOSABLE ELEMENTS; FETUS; GENE EXPRESSION; GENE THERAPY; GLOBINS; HUMANS; LIVER; MICE; MICE, INBRED C57BL; MICE, INBRED CBA; MICE, INBRED STRAINS; MICE, TRANSGENIC; POLYMERASE CHAIN REACTION; PROMOTER REGIONS (GENETICS); REPRODUCIBILITY OF RESULTS;

ADENO-ASSOCIATED VIRUS; ANIMALIA; MUS MUSCULUS; UNIDENTIFIED RETROVIRUS;

EID: 0030819839     PISSN: 03051048     EISSN: None     Source Type: Journal    
DOI: 10.1093/nar/25.6.1296     Document Type: Article

References (35)

1. Dillon, N. (1993) Trends Biotechnol., 11, 167-173.
2. Mulligan, R.C. (1993) Science, 260, 926-932.
3. Grosveld, F., van Assendelft, G.B., Greaves, D.R. and Kollias, G. (1987) Cell, 51, 975-985.
4. Gaensler, K.M., Kitamura, M. and Kan, Y.W. (1993) Proc. Natl. Acad. Sci. USA, 90, 11381-11385.
5. Peterson, K.R., Clegg, C.H., Huxley, C., Josephson, B.M., Haugen, H.S., Furukawa, T. and Stamatoyannopoulos, G. (1993) Proc. Natl. Acad. Sci. USA, 90, 7593-7597.
6. Ryan, T.M., Behringer, R.R., Martin, N.C., Townes, T.M., Palmiter, R.D. and Brinster, R.L. (1989) Genes Dev., 3, 314-323.
7. Tuan, D., Solomon, W., Li, Q. and London, I.M. (1985) Proc. Natl. Acad. Sci. USA, 82, 6384-6388.
8. Forrester, W.C., Thompson, C., Elder, J.T. and Groudine, M. (1986) Proc. Natl. Acad. Sci. USA, 83, 1359-1363.
9. Caterina, J.J., Ryan, T.M., Pawlik, K.M., Palmiter, R.D., Brinster, R.L., Behringer, R.R. and Townes, T.M. (1991) Proc. Natl. Acad. Sci. USA, 88, 1626-1630.
10. Talbot, D., Philipsen, S., Fraser, P. and Grosveld, F. (1990) EMBO J., 9, 2169-2177.
11. Talbot, D. and Grosveld, F. (1991) EMBO J., 10, 1391-1398.
12. Chang, J.C., Liu, D. and Kan, Y.W. (1992) Proc. Natl. Acad. Sci. USA, 89, 3107-3110.
13. Miller, J.L., Walsh, C.E., Ney, P.A., Samulski, R.J. and Nienhuis, A.W. (1993) Blood, 82, 1900-1906.
14. Novak, U., Harris, E.A., Forrester, W., Groudine, M. and Gelinas, R. (1990) Proc. Natl. Acad. Sci. USA, 87, 3386-3390.
15. Takekoshi, K.J., Oh, Y.H., Westerman, K.W., London, I.M. and Leboulch, P. (1995) Proc. Natl. Acad. Sci. USA, 92, 3014-3018.
16. Einerhand, M.P., Antoniou, M., Zolotukhin, S., Muzyczka, N., Berns, K.I., Grosveld, F. and Valerio, D. (1995) Gene Ther., 2, 336-343.
17. Leboulch, P., Huang, G.M., Humphries, R.K., Oh, Y.H., Eaves, C.J., Tuan, D.Y. and London, I.M. (1994) EMBO J., 13, 3065-3076.
18. Miller, J.L., Donahue, R.E., Sellers, S.E., Samulski, R.J., Young, N.S. and Nienhuis, A.W. (1994) Proc. Natl. Acad. Sci. USA, 91, 10183-10187.
19. Sadelain, M., Wang, C.H., Antoniou, M., Grosveld, F. and Mulligan, R.C. (1995) Proc. Natl. Acad. Sci. USA, 92, 6728-6732.
20. Plavec, I., Papayannopoulou, T., Maury, C. and Meyer, F. (1993) Blood, 81, 1384-1392.
21. Ren, S., Wong, B.Y., Li, J., Luo, X., Wong, P.M. and Atweh, G.F. (1996) Blood, 87, 2518-2524.
22. Miller, A.D. (1992) Nature, 357, 455-460.
23. Larochelle, A., Vormoor, J., Lapidot, T., Sher, G., Furukawa, T., Li, Q., Shultz, L.D., Olivieri, N.F., Stamatoyannopoulos, G. and Dick, J.E. (1995) Hum. Mol. Genet., 4, 163-172.
24. Ellis, J., Talbot, D., Dillon, N. and Grosveld, F. (1993) EMBO J., 12, 127-134.
25. Ellis, J. and Grosveld, F. (1993) Semin. Dev. Biol., 4, 359-369.
26. Philipsen, S., Pruzina, S. and Grosveld, F. (1993) EMBO J., 12, 1077-1085.
27. Strouboulis, J., Dillon, N. and Grosveld, F. (1992) Genes Dev., 6, 1857-1864.
28. Talbot, D., Collis, P., Antoniou, M., Vidal, M., Grosveld, F. and Greaves, D.R. (1989) Nature, 338, 352-355.
29. Ellis, J., Tan-Un, K.C., Harper, A., Michalovich, D., Yannoutsos, N., Philipsen, S. and Grosveld, F. (1996) EMBO J., 15, 562-568.
30. Fiering, S., Epner, E., Robinson, K., Zhuang, Y., Telling, A., Hu, M., Martin, D.I., Enver, T., Ley, T.J. and Groudine, M. (1995) Genes Dev., 9, 2203-2213.
31. McCune, S.L. and Townes, T.M. (1994) Nucleic Acids Res., 22, 4477-4481.
32. Wood, W.G. (1996) Trends Genet., 12, 204-206.
33. Bungert, J., Dave, U., Lim, K.C., Lieuw, K.H., Shavit, J.A., Liu, Q. and Engel, J.D. (1995) Genes Dev., 9, 3083-3096.
34. Milot, E., Strouboulis, J., Trimborn, T., Wijgerde, M., de Boer, E., Langeveld, A., Tan-Un, K., Vergeer, W., Yannoutsos, N., Grosveld, F. and Fraser, P (1996) Cell, 87, 105-114.
35. Wijgerde, M., Grosveld, F. and Fraser, P. (1995) Nature, 377, 209-213.