Effective treatment of familial hypercholesterolaemia in the mouse model using adenovirus-mediated transfer of the VLDL receptor gene

Nature Genetics

Volumn 13, Issue 1, 1996, Pages 54-62

  Kozarsky, Karen F ^a   Jooss, Karin ^a   Donahee, Mary ^a   Strauss III, Jerome F ^a   Wilson, James M ^b  

^a UNIVERSITY OF PENNSYLVANIA   (United States)

^b WISTAR INSTITUTE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

LOW DENSITY LIPOPROTEIN RECEPTOR; VERY LOW DENSITY LIPOPROTEIN;

ADENOVIRUS; ARTICLE; EXPRESSION VECTOR; FAMILIAL HYPERCHOLESTEROLEMIA; GENE EXPRESSION REGULATION; GENE TARGETING; GENE THERAPY; HUMAN; IMMUNE RESPONSE; PRIORITY JOURNAL; SEQUENCE HOMOLOGY;

ADENOVIRUSES, HUMAN; ANIMALS; BLOTTING, SOUTHERN; CHOLESTEROL; CYTOMEGALOVIRUS; DNA; GENE THERAPY; GENE TRANSFER TECHNIQUES; HUMANS; HYPERLIPOPROTEINEMIA TYPE II; LIVER; MICE; MICE, MUTANT STRAINS; PROMOTER REGIONS (GENETICS); RECEPTORS, LDL; RECOMBINATION, GENETIC; T-LYMPHOCYTES, CYTOTOXIC; VACCINIA VIRUS;

ADENOVIRIDAE; MURINAE;

EID: 0029988465     PISSN: 10614036     EISSN: None     Source Type: Journal    
DOI: 10.1038/ng0596-54     Document Type: Article

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