Correction of ornithine transcarbamylase deficiency in adult spfash mice and in OTC-deficient human hepatocytes with recombinant adenoviruses bearing the CAG promoter

Human Gene Therapy

Volumn 7, Issue 7, 1996, Pages 821-830

  Kiwaki, Kohji ^a   Kanegae, Yumi ^b   Saito, Izumu ^b   Komaki, Satoru ^a   Nakamura, Kimitoshi ^a   Miyazaki, Jun Ichi ^c   Endo, Fumio ^a   Matsuda, Ichiro ^a  

^a KUMAMOTO UNIVERSITY   (Japan)

^b UNIVERSITY OF TOKYO   (Japan)

^c UNIVERSITY OF TOKYO   (Japan)

Author keywords

[No Author keywords available]

Indexed keywords

ORNITHINE CARBAMOYLTRANSFERASE;

ACIDURIA; ADENOVIRUS; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CONTROLLED STUDY; ENZYME ACTIVITY; ENZYME DEFICIENCY; EXPRESSION VECTOR; GENE EXPRESSION; GENE TRANSFER; HUMAN; HUMAN CELL; HUMAN T CELL LEUKEMIA VIRUS 1; IMMUNOBLOTTING; LIVER CELL; MOUSE; NONHUMAN; PROMOTER REGION; PROTEIN EXPRESSION; RECOMBINANT GENE; SIMIAN VIRUS 40; TISSUE INJURY; VIRUS RECOMBINANT;

ACTINS; ADENOVIRIDAE; AMINO ACID METABOLISM, INBORN ERRORS; ANIMALS; ANTIBODIES; CELLS, CULTURED; DISEASE MODELS, ANIMAL; FEMALE; GENE THERAPY; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; HUMANS; IMMUNE SERA; LIVER; MALE; MICE; MICE, MUTANT STRAINS; ORNITHINE CARBAMOYLTRANSFERASE; OROTIC ACID; PROMOTER REGIONS (GENETICS); RECOMBINANT PROTEINS;

EID: 0029967430     PISSN: 10430342     EISSN: None     Source Type: Journal    
DOI: 10.1089/hum.1996.7.7-821     Document Type: Article

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