Adenoviral vectors for gene transfer of full-length human dystrophen cDNAs

Biochemical Society Transactions

Volumn 24, Issue 2, 1996, Pages

  Murphy, S ^a,b,c   Turner, G ^a,b,c   Piper, T ^a,b,c   Roberts, B ^a,b,c   Wadworth, S ^a,b,c   Smith, A E ^a,b,c   Wells, D J ^a,b,c   Dickson, G ^a,b,c  

^a UNIVERSITY OF LONDON   (United Kingdom)

^b GENZYME CORPORATION   (United States)

^c CHARING CROSS HOSPITAL   (United Kingdom)

Author keywords

[No Author keywords available]

Indexed keywords

DYSTROPHIN;

ADENOVIRUS; ANIMAL CELL; BECKER MUSCULAR DYSTROPHY; CONFERENCE PAPER; DUCHENNE MUSCULAR DYSTROPHY; GENE THERAPY; GENE TRANSFER; MOUSE; NEWBORN; NONHUMAN; PRIORITY JOURNAL; SKELETAL MUSCLE;

ADENOVIRIDAE; ANIMALS; CREATINE KINASE; DEFECTIVE VIRUSES; DNA, COMPLEMENTARY; DYSTROPHIN; GENE DELETION; GENE THERAPY; GENES, VIRAL; GENETIC VECTORS; HUMANS; ISOENZYMES; MICE; MICE, INBRED MDX; MUSCULAR DYSTROPHIES; MUSCULAR DYSTROPHY, ANIMAL; RECOMBINANT FUSION PROTEINS; REPETITIVE SEQUENCES, NUCLEIC ACID; TRANSFECTION; VIRUS REPLICATION;

ADENOVIRIDAE; ANIMALIA;

EID: 0029933613     PISSN: 03005127     EISSN: None     Source Type: Journal    
DOI: None     Document Type: Article

References (8)

1. Emery, A. E. H. 1993. Duchenne Muscular Dystrophy. 2nd edition, Oxford University Press, Oxford, UK.
2. Perricaudet, M. and L. D. Stratford-Perricaudet. 1995. Ch1. Adenovirus-mediated in vivo gene therapy. In Viruses in human gene therapy. J. M. H. Vos, editor. Chapman and Hall, London. 1-32.
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7. Yang, Y., F. A. Nunes, K. Berensci, E. Gönczol, J. F. Engelhardt and J. M. Wilson. 1994b. Inactivation of E2a in recombinant adenoviruses improves the prospect for gene therapy for cystic fibrosis. Nat. Genet. 7:362-369.
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