Gene therapy for metachromatic leukodystrophy

Pediatrics International

Volumn 38, Issue 2, 1996, Pages 193-201

  Ohashi, Toya ^a   Watabe, Kazuhiko ^a   Sato, Yumi ^b   Saito, Izumu ^b   Barranger, John A ^c   Matalon, Reuben ^d   Eto, Yoshikatsu ^a  

^a JIKEI UNIVERSITY SCHOOL OF MEDICINE   (Japan)

^b UNIVERSITY OF TOKYO   (Japan)

^c UNIVERSITY OF PITTSBURGH   (United States)

^d MIAMI CHILDREN'S HOSPITAL   (United States)

Author keywords

Adenovirus; Gene therapy; Metachromatic leukodystrophy; Retrovirus; Sulfatase

Indexed keywords

CEREBROSIDE SULFATASE; GLYCOSAMINOGLYCAN; N ACETYLGALACTOSAMINE 4 SULFATASE; VIRUS VECTOR;

ADENOVIRUS; CONTROLLED STUDY; ENZYME ACTIVITY; ENZYME DEFICIENCY; GENE EXPRESSION; GENE THERAPY; HUMAN; HUMAN CELL; METACHROMATIC LEUKODYSTROPHY; PRIORITY JOURNAL; RETROVIRUS; REVIEW; VIRUS RECOMBINANT;

ADENOVIRIDAE; BRAIN; CEREBROSIDE-SULFATASE; GENE EXPRESSION; GENE THERAPY; GENETIC VECTORS; GLYCOSAMINOGLYCANS; HUMANS; LEUKODYSTROPHY, METACHROMATIC; LYSOSOMES; OLIGODENDROGLIA; RETROVIRIDAE; SULFATASES;

EID: 0029919605     PISSN: 13288067     EISSN: 1442200X     Source Type: Journal    
DOI: 10.1111/j.1442-200X.1996.tb03468.x     Document Type: Article

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