Expression of the human multidrug resistance and glucocerebrosidase cDNAs from adeno-associated vectors: Efficient promoter activity of AAV sequences and in vivo delivery via liposomes

Human Gene Therapy

Volumn 7, Issue 11, 1996, Pages 1309-1322

  Baudard, Marion ^a,e   Flotte, Terence R ^b   Aran, Josep M ^a   Thierry, Alain R ^a,f   Pastan, Ira ^a   Pang, Myung Geol ^c   Kearns, William G ^c,d   Gottesman, Michael M ^a  

^a NATIONAL CANCER INSTITUTE   (United States)

^b JOHNS HOPKINS HOSPITAL   (United States)

^c CENTER FOR PEDIATRIC RESEARCH   (United States)

^d JOHNS HOPKINS UNIVERSITY SCHOOL OF MEDICINE   (United States)

^e HÔTEL DIEU   (France)

^f TRANSGENE S A   (France)

Author keywords

[No Author keywords available]

Indexed keywords

COMPLEMENTARY DNA; GLUCOSYLCERAMIDASE; GLYCOPROTEIN P; LIPOSOME;

ADENO ASSOCIATED VIRUS; ANIMAL CELL; ARTICLE; DRUG EFFECT; EFFUSION; EXPRESSION VECTOR; GENE; GENE SEQUENCE; GENE THERAPY; LONG TERMINAL REPEAT; MOUSE; MULTIDRUG RESISTANCE; NONHUMAN; PHENOTYPE; PLASMID;

EID: 0029797538     PISSN: 10430342     EISSN: None     Source Type: Journal    
DOI: 10.1089/hum.1996.7.11-1309     Document Type: Article

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