Engraftment of gene–modified umbilical cord blood cells in neonates with adenosine deaminase deficiency

Nature Medicine

Volumn 1, Issue 10, 1995, Pages 1017-1023

  Kohn, Donald B ^a,b   Weinberg, Kenneth I ^a,b   Nolta, Jan A ^a,b   Heiss, Linda N ^a,b   Lenarsky, Carl ^a,b   Crooks, Gay M ^a,b   Hanley, Mary E ^a,b   Annett, Geralyn ^a,b   Brooks, Judith S ^a,b   El Khoureiy, Anthony ^a,b   Lawrence, Kim ^a,b   Wells, Susie ^a,b   Moen, Robert C ^c   Bastian, John ^d   Williams Herman, Debora E ^e   Elder, Melissa ^e   Wara, Diane ^e   Bowen, Thomas ^f   Hershfield, Michael S ^g   Mullen, Craig A ^h   Blaese, R Michael ^h   Parkman, Robertson ^a,b   more..

^a CHILDREN S HOSPITAL LOS ANGELES   (United States)

^b UNIVERSITY OF SOUTHERN CALIFORNIA   (United States)

^c NOVARTIS PHARMA AG   (Switzerland)

^d RADY CHILDREN'S HOSPITAL   (United States)

^e UNIVERSITY OF CALIFORNIA   (United States)

^f Duke University Medical Center ^*  (Canada)

^g DUKE UNIVERSITY MEDICAL CENTER   (United States)

^h NATIONAL HUMAN GENOME RESEARCH INSTITUTE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ADENOSINE DEAMINASE; GENE PRODUCT;

ADENOSINE DEAMINASE DEFICIENCY; ARTICLE; BLOOD TRANSFUSION; CASE REPORT; CLINICAL TRIAL; COMBINED IMMUNODEFICIENCY; GENE THERAPY; HUMAN; NEWBORN; PRIORITY JOURNAL; UMBILICAL CORD BLOOD;

ADENOSINE DEAMINASE; ANTIGENS, CD34; BASE SEQUENCE; BLOOD TRANSFUSION, AUTOLOGOUS; BONE MARROW; DNA PRIMERS; FEMALE; FETAL BLOOD; GENE THERAPY; GENETIC VECTORS; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HEMATOPOIETIC STEM CELLS; HUMAN; INFANT, NEWBORN; LEUKOCYTES; LYMPHOCYTE TRANSFUSION; MALE; MOLECULAR SEQUENCE DATA; RETROVIRIDAE; SEVERE COMBINED IMMUNODEFICIENCY; TRANSDUCTION, GENETIC;

EID: 0028864561     PISSN: 10788956     EISSN: 1546170X     Source Type: Journal    
DOI: 10.1038/nm1095-1017     Document Type: Article

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