A pilot study of ex vivo gene therapy for homozygous familial hypercholesterolaemia

Nature Medicine

Volumn 1, Issue 11, 1995, Pages 1148-1154

  Grossman, Mariann ^a   Rader, Daniel J ^a   Muller, David W M ^b   Kolansky, Daniel M ^a   Kozarsky, Karen ^a   Clark, Bernard J ^a   Stein, Evan A ^c   Lupien, Paul J ^d   Brewer, H Bryan ^e   Raper, Steven E ^a   Wilson, James M ^a  

^a HOSPITAL OF THE UNIVERSITY OF PENNSYLVANIA   (United States)

^b UNIVERSITY OF MICHIGAN HEALTH SYSTEM   (United States)

^c CHRIST HOSPITAL   (United States)

^d UNIVERSITÉ LAVAL   (Canada)

^e NATIONAL HEART LUNG AND BLOOD INSTITUTE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ADULT; ARTICLE; CASE REPORT; CHILD; CLINICAL TRIAL; FAMILIAL HYPERCHOLESTEROLEMIA; FEMALE; GENE THERAPY; HUMAN; MALE; PRIORITY JOURNAL;

ADULT; ANTIBODY FORMATION; CELL TRANSPLANTATION; CELLS, CULTURED; CHILD; CHOLESTEROL; FEMALE; FOLLOW-UP STUDIES; GENE THERAPY; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; HETEROZYGOTE; HUMAN; HYPERCHOLESTEROLEMIA, FAMILIAL; IN SITU HYBRIDIZATION; LIPIDS; LIPOPROTEINS, LDL; LIVER; MALE; PILOT PROJECTS; RECEPTORS, LDL; SUPPORT, U.S. GOV'T, P.H.S.; TREATMENT OUTCOME;

EID: 0028793489     PISSN: 10788956     EISSN: 1546170X     Source Type: Journal    
DOI: 10.1038/nm1195-1148     Document Type: Article

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