Gene therapy in the treatment of disease

The Journal of Allergy and Clinical Immunology

Volumn 94, Issue 6 PART 1, 1994, Pages 942-951

  Dickler, Howard B ^a   Collier, Elaine ^a  

^a NATIONAL INSTITUTE OF ALLERGY AND INFECTIOUS DISEASES   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ADENOSINE DEAMINASE;

ACQUIRED IMMUNE DEFICIENCY SYNDROME; CANCER; CONFERENCE PAPER; CYSTIC FIBROSIS; ENZYME DEFICIENCY; GENE THERAPY; GENOME; HEMOPHILIA; HUMAN; KIDNEY FAILURE; MUSCULAR DYSTROPHY; PRIORITY JOURNAL; RESEARCH;

ACQUIRED IMMUNODEFICIENCY SYNDROME; ADENOSINE DEAMINASE; CYSTIC FIBROSIS; GENE THERAPY; HEMOPHILIA A; HUMAN; HUMAN GENOME PROJECT; KIDNEY FAILURE; MUSCULAR DYSTROPHIES; NEOPLASMS;

EID: 0028650383     PISSN: 00916749     EISSN: None     Source Type: Journal    
DOI: 10.1016/0091-6749(94)90111-2     Document Type: Article

References (25)

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7. The structural and functional diversity of dystrophin
8. The potential for gene therapy in Duchenne muscular dystrophy and other genetic muscle diseases
9. Long-term correction of mouse dystrophic degeneration by adenovirusmediated transfer of a minidystrophin gene
10. The ADA human gene therapy clinical protocol
11. Gene therapy for primary immunodeficiency
12. Development of gene therapy for immunodeficiency: adenosine deaminase deficiency
13. Phase I study of cytokine gene modified autologous neuroblastoma cells for treatment of relapsed/refractory neuroblastoma
14. Gene-marking to trace origin of relapse after autologous bone-marrow transplantation
15. Molecular mechanisms of CFTR chloride channel dysfunction in cystic fibrosis
16. Correction of the cystic fibrosis defect in vitro by retrovirus-mediated gene transfer
17. Expression of cystic fibrosis transmembrane conductance regulator corrects defective chloride channel regulation in cystic fibrosis airway epithelial cells
18. In vivo transfer of the human cystic fibrosis transmembrane conductance regulator gene to the airway epithelium
19. Direct gene transfer of human CFTR into human bronchial epithelia of xenografts with E1-deleted adenoviruses
20. Development and analysis of recombinant adenoviruses for gene therapy of cystic fibrosis
21. Gene transfer to freshly isolated human respiratory epithelial cells in vivo using a replication deficient adenovirus containing the human cystic fibrosis transmembrane conductance regulator cDNA
22. Adenovirus-mediated gene transfer transiently corrects the chloride transport defect in nasal epithelia of patients with cystic fibrosis
23. Systemic delivery of recombinant proteins using genetically modified myoblasts
24. Biochemistry of multidrug resistance mediated by the multidrug transporter
25. Drug-selected coexpression of human glucocerebrosidase and P-glycoprotein using a bicistronic vector