Replacement therapy for inherited enzyme deficiency — macrophage-targeted glucocerebrosidase for gaucher's disease

New England Journal of Medicine

Volumn 324, Issue 21, 1991, Pages 1464-1470

  Barton, Norman W ^a   Brady, Roscoe O ^a   Murray, Gary J ^a   Argoff, Charles E ^a   Grewal, Raji P ^a   yu, Kian ti ^a   Dambrosia, James M ^a   di Bisceglie, Adrian M ^b   Hill, Suvimol C ^a   Parker, Robert I ^a   Doppelt, Samuel H ^c   Mankin, Henry J ^c  

^a NATIONAL INSTITUTES OF HEALTH   (United States)

^b NATIONAL INSTITUTE OF NEUROLOGICAL DISORDERS AND STROKE   (United States)

^c MASSACHUSETTS GENERAL HOSPITAL   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ACID PHOSPHATASE; ALGLUCERASE; GLUCOSYLCERAMIDASE; HEMOGLOBIN;

ADOLESCENT; ADULT; ARTICLE; CLINICAL ARTICLE; DRUG EFFICACY; ENZYME DEFICIENCY; FEMALE; GAUCHER DISEASE; HEREDITY; HUMAN; INBORN ERROR OF METABOLISM; INTRAVENOUS DRUG ADMINISTRATION; MALE; PRIORITY JOURNAL; SCHOOL CHILD; THROMBOCYTE COUNT;

ACID PHOSPHATASE; ADOLESCENT; ADULT; BONE DEVELOPMENT; CHILD; FEMALE; GAUCHER DISEASE; GLUCOSYLCERAMIDASE; GLUCOSYLCERAMIDES; HEMOGLOBINS; HUMAN; MACROPHAGES; MALE; ORGAN WEIGHT; SPLEEN; SUPPORT, NON-U.S. GOV'T;

EID: 0025869216     PISSN: 00284793     EISSN: 15334406     Source Type: Journal    
DOI: 10.1056/NEJM199105233242104     Document Type: Article

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